Weekly shot shows promise for helping kids with dwarfism grow

NCT ID NCT05929807

First seen Nov 01, 2025 · Last updated May 06, 2026 · Updated 30 times

Summary

This study tests a once-weekly injection called TransCon CNP in children and teens with achondroplasia, the most common form of dwarfism. The goal is to see if it is safe and helps improve growth over several years. Participants who were in a previous TransCon CNP trial can join, and treatment continues until their growth plates close.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for ACHONDROPLASIA are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • Ascendis Investigational Site

    Aurora, Colorado, 80045, United States

  • Ascendis Investigational Site

    Wilmington, Delaware, 19803, United States

  • Ascendis Investigational Site

    Saint Paul, Minnesota, 55102, United States

  • Ascendis Investigational Site

    Houston, Texas, 77030, United States

  • Ascendis Investigational Site

    Linz, 4020, Austria

  • Ascendis Investigational Site

    Montreal, H3T 1C5, Canada

  • Ascendis Investigational Site

    Berlin, 13353, Germany

  • Ascendis Investigational Site

    Auckland, 1023, New Zealand

  • Ascendis Investigational Site

    Coimbra, 3000-602, Portugal

  • Ascendis Investigational Site

    Vitoria-Gasteiz, 1008, Spain

  • Ascendis Pharma Investigational Site

    Little Rock, Arkansas, 72202, United States

  • Ascendis Pharma Investigational Site

    Columbia Falls, Montana, 65212, United States

  • Ascendis Pharma Investigational Site

    Buffalo, New York, 14203, United States

  • Ascendis Pharma Investigational Site

    Madison, Wisconsin, 53705, United States

  • Ascendis Pharma Investigational Site

    Parkville, Victoria, 3052, Australia

  • Ascendis Pharma Investigational Site

    Copenhagen, 2100, Denmark

  • Ascendis Pharma Investigational Site

    Dublin, D01 YC76, Ireland

Conditions

Explore the condition pages connected to this study.