Cream trial aims to smooth facial bumps in rare genetic disorder
NCT ID NCT03363763
Summary
This study tested whether a cream containing the drug sirolimus could safely reduce the facial bumps (angiofibromas) common in children with tuberous sclerosis complex (TSC). About 45 children and young adults applied one of two strengths of the cream or a placebo cream to their face nightly for 12 weeks. The main goal was to see if the treatment improved the appearance and severity of these skin growths.
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Contacts and locations
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Locations
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Boston Children's Hospital
Boston, Massachusetts, 02115, United States
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Children's Clinical Research Organization, Children's Hospital Colorado
Aurora, Colorado, 80045, United States
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Children's Healthcare of Atlanta
Atlanta, Georgia, 30329, United States
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Children's Hospital of Fudan University
Shanghai, 201102, China
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Children's Hospital of Los Angeles, Division of Neurology
Los Angeles, California, 90027, United States
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Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
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LeBonheur Children's Hospital
Memphis, Tennessee, 38103, United States
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Translational Genomics Research
Phoenix, Arizona, 85004, United States
Conditions
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