Major drug trial for Muscle-Weakening disease halted after just 6 patients

NCT ID NCT05132569

Summary

This study aimed to test whether an oral drug called tolebrutinib could help control symptoms and improve daily life for adults with moderate-to-severe generalized myasthenia gravis (gMG), a chronic autoimmune disease that causes muscle weakness. It was a large Phase 3 trial designed to compare the drug against a placebo over 26 weeks, followed by a longer-term extension. However, the trial was terminated very early, enrolling only 6 participants, so no conclusions about the drug's effectiveness for gMG could be drawn from this study.

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Contacts and locations

Locations

  • Georgetown University-Site Number:8400008

    Washington D.C., District of Columbia, 20007, United States

  • Harvard Medical School - Brigham and Women's Hospital-Site Number:8400004

    Boston, Massachusetts, 02115, United States

  • Investigational Site Number :1240003

    London, Ontario, N6A 5A5, Canada

  • Investigational Site Number :1240004

    Edmonton, Alberta, T6G 2B7, Canada

  • Investigational Site Number :1560001

    Shanghai, 200040, China

  • Investigational Site Number :1560002

    Wuhan, 430030, China

  • Investigational Site Number :1560003

    Chengdu, 610041, China

  • Investigational Site Number :3480001

    Szeged, 6725, Hungary

  • Investigational Site Number :3480002

    Pécs, 7623, Hungary

  • Investigational Site Number :3800001

    Milan, 20132, Italy

  • Investigational Site Number :3800002

    Milan, Lombardy, 20133, Italy

  • Investigational Site Number :3800003

    Roma, 00168, Italy

  • Investigational Site Number :3800004

    Naples, 80131, Italy

  • Investigational Site Number :3920002

    Sagamihara-shi, Kanagawa, 252-0392, Japan

  • Investigational Site Number :6160001

    Zabrze, 41-800, Poland

  • Investigational Site Number :7240003

    L'Hospitalet de Llobregat, Catalunya [Cataluña], 08907, Spain

  • Investigational Site Number :7240005

    Madrid, Madrid, Comunidad de, 28046, Spain

  • Investigational Site Number :8260001

    Liverpool, L9 7LJ, United Kingdom

  • Investigational Site Number :8260002

    Exeter, Devon, EX2 5DW, United Kingdom

  • Neurology Center of San Antonio, PA-Site Number:8400009

    San Antonio, Texas, 00000, United States

  • SFM Clinical Research, LLC-Site Number:8400006

    Boca Raton, Florida, 33487, United States

  • University of South Florida Health- Morsani Center for Advanced Healthcare-Site Number:8400001

    Tampa, Florida, 33612-6601, United States

Conditions

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