New hope for kids with rare hormone disorder: drug may cut steroid doses
NCT ID NCT05128942
First seen Jan 11, 2026 · Last updated Apr 25, 2026 · Updated 19 times
Summary
This study tested a drug called tildacerfont in children aged 2 to 17 with congenital adrenal hyperplasia (CAH), a condition where the body can't make certain hormones properly. The goal was to see if the drug is safe and can help control the disease while allowing children to take lower doses of their usual steroid medications. The study was stopped early, so results are limited.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Spruce Study Site
Sacramento, California, 95821, United States
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Spruce Study Site
San Diego, California, 92123, United States
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Spruce Study Site
Chicago, Illinois, 60611, United States
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Spruce Study Site
Minneapolis, Minnesota, 55454, United States
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Spruce Study Site
Buffalo, New York, 14203, United States
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Spruce Study Site
Providence, Rhode Island, 02903, United States
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Spruce Study Site
Columbia, South Carolina, 29203, United States
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Spruce Study Site
Dallas, Texas, 75231, United States
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Spruce Study Site
Edinburg, Texas, 78539, United States
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Spruce Study Site
Fort Worth, Texas, 76104, United States
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Spruce Study Site
Salt Lake City, Utah, 84113, United States
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Spruce Study Site
Charlottesville, Virginia, 22903, United States
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Spruce Study Site
Richmond, Virginia, 23284, United States
Conditions
Explore the condition pages connected to this study.