Desperate hope: stem cells tested on one child with rare muscle disease
NCT ID NCT05154851
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This trial gives a single child with a rare form of congenital muscular dystrophy access to their own banked stem cells. The cells are given through 14 IV infusions to see if they are safe and can help control the disease. Because it involves only one patient, the results will be very limited.
What this could mean
Our plain-language read of the trial. This is informational only — not medical advice or a prediction.
Active substance
autologous adipose-derived mesenchymal stem cells (HB-adMSCs)
What this could lead to
If successful, this could point toward a way to slow or manage congenital muscular dystrophy in this patient.
What could go wrong
This is a single-patient expanded access study, not a full clinical trial. Results may not apply to others, and risks include infection or infusion reactions.
Disclaimer
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This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Locations
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Hope Biosciences Stem Cell Research Foundation
Sugar Land, Texas, 77478, United States