Early trial tests stem cell particles for rare Muscle-Weakening disorder

NCT ID NCT07226726

Summary

This early-stage study is testing whether a solution containing particles from stem cells (called exosomes) can help people with congenital myasthenic syndrome, a rare genetic disorder that causes muscle weakness. The trial will enroll 20 participants to see if the treatment is safe and to measure changes in their oxygen levels. This is a first step to see if the approach has potential before larger studies are conducted.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Medical Surgical Associates Center

    RECRUITING

    St John's, Antigua and Barbuda

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Prodromos Stem Cell Institute

    RECRUITING

    Naples, Florida, 34102, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Prodromos Stem Cell Institute

    RECRUITING

    Irving, Texas, 75039, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.