Real-World data reveals how kids with SMA are treated outside clinical trials
NCT ID NCT07474311
First seen Mar 20, 2026 · Last updated May 03, 2026 · Updated 7 times
Summary
This study analyzed medical records of 213 children with spinal muscular atrophy (SMA) in the Czech and Slovak Republics to see how treatments are actually used in everyday practice. Researchers tracked motor skills, breathing, feeding, and other health measures over time. The goal was to understand real-world outcomes, not to test a new drug.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Novartis
Prague, 140 00, Czechia
Conditions
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