Massive data dive reveals true cost of treating rare muscle disease

NCT ID NCT07378943

Summary

This study aimed to understand how three different treatments for spinal muscular atrophy (SMA) are actually used in the real world and what they cost the healthcare system. Researchers analyzed anonymous insurance claims data from over 4,100 patients who received one of the treatments between 2016 and 2024. The goal was to gather practical information on dosing patterns and long-term expenses, not to test a new therapy.

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Contacts and locations

Locations

  • Novartis

    East Hanover, New Jersey, 07936, United States

Conditions

Explore the condition pages connected to this study.