Massive study reveals how SMA patients fare on modern drugs

NCT ID NCT07403214

Summary

This study looked back at the real-world experiences of 4,805 people with spinal muscular atrophy (SMA) who received one or more of three modern drug treatments. It aimed to understand how often patients needed hospital care or special medical equipment before and after starting treatment. By analyzing health insurance claims data, researchers tracked treatment patterns and health outcomes to learn how these drugs perform outside of controlled clinical trials.

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Contacts and locations

Locations

  • Novartis

    East Hanover, New Jersey, 07936, United States

Conditions

Explore the condition pages connected to this study.