One-Shot gene therapy aims to cure devastating blood disease

NCT ID NCT06565026

Summary

This early-stage study is testing a potential one-time treatment for severe sickle cell disease. Doctors will collect a patient's own blood stem cells, edit a specific gene in the lab to boost protective fetal hemoglobin, and then return the cells. The goal is to see if this single treatment is safe and can effectively control or cure the disease by reducing painful crises and the need for ongoing care.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • The First Affiliated Hospital of Guangxi Medical University

    RECRUITING

    Nanning, Guangxi, China

    Contact

    Contact

Conditions

Explore the condition pages connected to this study.