Scientists track patients for 15 years after revolutionary gene therapy

NCT ID NCT06155500

Summary

This study is following 4 patients for 15 years after they received an experimental gene therapy for sickle cell disease. The therapy involves editing a patient's own blood stem cells to produce fetal hemoglobin, which can help control the disease. Researchers are monitoring long-term safety and whether the treatment effects last over time.

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Contacts and locations

Locations

  • Memorial Sloan Kettering Cancer Ctr

    New York, New York, 10065, United States

  • St Jude Childrens Research Hospital

    Memphis, Tennessee, 38105, United States

  • University of Chicago

    Chicago, Illinois, 60637, United States

Conditions

Explore the condition pages connected to this study.