New pill aims to boost blood health and cut pain crises in sickle cell

NCT ID NCT04624659

Summary

This study is testing whether a new oral medication called etavopivat can help people with sickle cell disease. It aims to increase healthy hemoglobin levels in the blood and reduce the frequency of painful vaso-occlusive crises. The trial involves 450 participants aged 12 to 65 and compares the medication against a placebo over a year of treatment.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for SICKLE CELL DISEASE are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • 'Ippokrateio' General Hospital of Thessaloniki

    Thessaloniki, 54642, Greece

  • ARNAS Ospedali Civico Di Cristina Benfratelli - Presidio Ospedaliero "Civio e Benfratelli"

    Palermo, 90127, Italy

  • Adana City Training and Research Hospital

    Adana, 4522, Turkey (Türkiye)

  • Advanced Pharma CR

    Miami, Florida, 33147, United States

  • Ain Shams University Hospital

    Cairo, 1181, Egypt

  • Al Kasr AL Aini Hospital

    Cairo, 11956, Egypt

  • All India Institute of Medical Sciences (AIIMS)

    New Delhi, 110029, India

  • American University of Beirut Medical center

    Beirut, 11-0236, Lebanon

  • Aminu Kano Teaching Hospital (AKTH)

    Kano, 3452, Nigeria

  • Ap-Hp-Hopital Henri Mondor

    Créteil, 94010, France

  • Ap-Hp-Hopital Robert Debre

    Paris, 75019, France

  • Arnold Palmer Children's Hospital

    Orlando, Florida, 32806, United States

  • Azienda Ospedale Universita Padova

    Padua, 35128, Italy

  • Azienda Ospedaliera Universitaria San Luigi Gonzaga - S.C.D.O. Microcitemie e malattie rare ematologiche

    Orbassano, 10043, Italy

  • Azienda Ospedaliero Universitaria Policlinico G. Rodolico - San Marco

    Catania, 95123, Italy

  • Barau Dikko Teaching Hospital, Kaduna

    Kaduna, 800212, Nigeria

  • Başkent Üniversitesi Adana Dr. Turgut Noyan Uygulama ve Araştırma Merkezi

    Adana, 1240, Turkey (Türkiye)

  • Boston Medical Center

    Boston, Massachusetts, 02118, United States

  • CHU Sainte-Justine Mother and Child University Hospital

    Montreal, Quebec, H3T 1C5, Canada

  • Cairo University

    Cairo, 111111, Egypt

  • Center for Blood Disorders Augusta University

    Augusta, Georgia, 30912, United States

  • Centre Hospitalier Universitaire de Montpellier-Hopital Saint-Eloi

    Montpellier, 34295, France

  • Centro per lo Studio e la Cura delle Amiloidosi Sistemiche Fondazione IRCCS Policlinico San Matteo

    Pavia, PV, 27100, Italy

  • Charité - Campus Virchow-Klinikum - Klinik für Pädiatrie mit Schwerpunkt Onkologie und Hämatologie

    Berlin, 13353, Germany

  • Children's Healthcare of Atlanta Investigational Medication Pharmacy

    Atlanta, Georgia, 30342, United States

  • Children's Hosp-New Orleans

    New Orleans, Louisiana, 70118, United States

  • Children's Hosptl Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

  • Children's National Health Hospital

    Washington, New Jersey, 20010, United States

  • Churchill Hospital

    Oxford, OX3 7LE, United Kingdom

  • Columbia University Medical Center_New York

    New York, New York, 10032, United States

  • Complejo Hospitalario Universitario A Coruña

    A Coruña, 15006, Spain

  • Cornerstone Research Institute

    Altamonte Springs, Florida, 32701, United States

  • Duke University Medical Center

    Durham, North Carolina, 27710, United States

  • East Carolina University

    Greenville, North Carolina, 27858, United States

  • Ege Üniversitesi Tip Fakultesi Hastanesi - Nefroloji

    Izmir, 35040, Turkey (Türkiye)

  • Emory University School of Medicine

    Atlanta, Georgia, 30303, United States

  • Foundation for Sickle Cell Disease Research

    Hollywood, Florida, 33023, United States

  • GHR Mulhouse Sud-Alsace

    Mulhouse, 68100, France

  • Gen Hosp Athens Ippokrateio,B' Uni Clinic Internal Medicine

    Athens, 115 27, Greece

  • General Hospital Of Larissa Koutlibaneio And Triantafylleio - Thalassemia and SCD Unit

    Larissa, 41221, Greece

  • General University Hospital of Patras

    Pátrai, Larissa, 265 04, Greece

  • Gertrude's Children's Hospital, Nairobi

    Nairobi, 100, Kenya

  • Ghana Institute of Clinical Genetics, Korle Bu Teaching Hospital (KBTH)

    Accra, 0, Ghana

  • Guys and St Thomas NHS Foundation Trust / Evelina Childrens Hospital

    London, SE18 3RA, United Kingdom

  • Hacettepe Üniversitesi Hastanesi- Hematoloji

    Ankara, 6230, Turkey (Türkiye)

  • Hammersmith Hospital - London

    London, W2 1NY, United Kingdom

  • Hospices Civils de Lyon-Hopital Edouard Herriot

    Lyon, 69437, France

  • Hospital Clinico San Carlos

    Madrid, 28040, Spain

  • Hospital Germans Trias i Pujol

    Badalona, 8916, Spain

  • Hospital Gregorio Marañón

    Madrid, 28009, Spain

  • Hospital Nini

    Tripoli, 113-6044, Lebanon

  • Hospital Ramón y Cajal

    Madrid, 28034, Spain

  • Hospital Sant Joan de Déu

    Barcelona, 8950, Spain

  • Hospital Universitario La Paz

    Madrid, 28046, Spain

  • Hospital Universitario Virgen del Rocío

    Seville, 41013, Spain

  • Hospital Universitario de Cruces

    Barakaldo, 48903, Spain

  • Hospital Vall d'Hebron

    Barcelona, 08035, Spain

  • Howard University

    Washington D.C., District of Columbia, 20060, United States

  • Jacobi Medical Center

    The Bronx, New York, 10461, United States

  • Jimmy Everest Cancer Hematology & Oncology

    Oklahoma City, Oklahoma, 73104, United States

  • K.J Somaiya Hospital and Research Centre

    Mumbai, Maharashtra, 400022, India

  • KEMRI Kondele Children Hospital, Kisumu

    Kisumu, 40100, Kenya

  • KEMRI Siaya Clinical Research Annex Siaya County Referral Hospital, Siaya

    Kisumu, 40600, Kenya

  • Karmanos Cancer Institute

    Detroit, Michigan, 48201, United States

  • King Fahad Specialist Hospital-Dammam

    Dammam, 32253, Saudi Arabia

  • King Khaled University Hospital,King Saud Univ. Med. City

    Riyadh, 12372 6864, Saudi Arabia

  • Kings College Hospital - Haematology

    London, SE5 9RS, United Kingdom

  • Kintampo Health Research Centre (KHRC), Kintampo, Ghana

    Kintampo, 200, Ghana

  • Kombewa Clinical Research Centre

    Kisumu, 1932, Kenya

  • Lagos University Teaching Hospital, Lagos

    Lagos, 102215, Nigeria

  • Leicester Royal Infirmary - Haemostasis & Thrombosis Unit

    Leicester, LE1 5WW, United Kingdom

  • Levine Cancer Institute

    Charlotte, North Carolina, 28204, United States

  • Lynn Institute of Tulsa

    Tulsa, Oklahoma, 74135, United States

  • Mary Bridge Children's Health

    Tacoma, Washington, 98405, United States

  • Massachusetts General Hospital_Boston

    Boston, Massachusetts, 02114, United States

  • Master Centre for Lebanon

    Amman, 11844, Lebanon

  • Medical University of South Carolina

    Charleston, South Carolina, 29425, United States

  • Mersin Üniversitesi Tip Fakültesi Hastanesi- Çiftlikköy Yerleşkesi- Hematoloji

    Mersin, 33110, Turkey (Türkiye)

  • Methodist University Hospital

    Memphis, Tennessee, 38104, United States

  • Montefiore Medical Center

    The Bronx, New York, 10467, United States

  • NYC Health+Hospitals

    Brooklyn, New York, 11203, United States

  • Neuro-Behavioral Clinical Research

    North Canton, Ohio, 44720, United States

  • North Shore Long Island Jewish Medical Center

    New Hyde Park, New York, 11040, United States

  • Ospedale Pediatrico Bambino Ges

    Roma, 00165, Italy

  • Pacific Research Partners

    Oakland, California, 94607, United States

  • Phoenix Children's Hsptl

    Phoenix, Arizona, 85016, United States

  • Prince Mohammad Bin Naser Hospital

    Jizan, 82943, Saudi Arabia

  • Prisma Health-Upstate

    Greenville, South Carolina, 29605, United States

  • Providence Hematolgy

    Vancouver, British Columbia, V6E 1M7, Canada

  • Queens Hospital Center

    Jamaica, New York, 11432-1121, United States

  • Rhode Island Hospital

    Providence, Rhode Island, 02903, United States

  • Royal Hallamshire Hospital

    Sheffield, S11 8RN, United Kingdom

  • Saint-Denis Hospital Center

    Saint-Denis, 93200, France

  • Sonar Clinical Research

    Atlanta, Georgia, 30315, United States

  • Srirama Chandra Bhanj Medical College & Hospital (S.C.B Medical College)

    Cutack, 753007, India

  • Sultan Qaboos University Hospital

    Muscat, Sultanet of Oman/Muscat/Al Khoud, 123, Oman

  • Sydnawy University Hospital

    Zagazig, 44519, Egypt

  • The Hospital for Sick Children

    Toronto, Ontario, M5G 1X8, Canada

  • The Ohio State University Medical Center

    Columbus, Ohio, 43203, United States

  • Thomas Jefferson University Hospital

    Philadelphia, Pennsylvania, 19107, United States

  • UC Davis Medical Center

    Sacramento, California, 95817, United States

  • UCSF Oakland Benioff ChildHosp

    Oakland, California, 94609, United States

  • UT Health University of Texas

    Houston, Texas, 77030, United States

  • Uniklinik Heidelberg - Klinik für Pädiatrische Onkologie, Hämatologie, Immunologie und Pneumologie

    Heidelberg, 69120, Germany

  • Univ of Alabama Birmingham

    Birmingham, Alabama, 35233, United States

  • University Health Network - Toronto General Hospital

    Toronto, Ontario, M5G 2C4, Canada

  • University Hospital Lewisham, Lewisham and Greenwich NHS Trust

    London, SE13 6LH, United Kingdom

  • University Of California Irvine

    Orange, California, 92868, United States

  • University Of Maryland School of Medicine

    Baltimore, Maryland, 21201, United States

  • University Of Miami

    Miami, Florida, 33136, United States

  • University of Abuja Teaching Hospital, Gwagwalada, Abuja

    Abuja, 228, Nigeria

  • University of Cincinnati

    Cincinnati, Ohio, 45219, United States

  • University of Connecticut

    Farmington, Connecticut, 06030, United States

  • University of Florida

    Gainesville, Florida, 32610, United States

  • University of Illinois at Chicago

    Chicago, Illinois, 60612, United States

  • University of Nebraska Medical Center

    Omaha, Nebraska, 68198-2168, United States

  • University of Nigeria Teaching Hospital, Enugu

    Lagos, 102215, Nigeria

  • University of Pittsburgh Medical Center

    Pittsburgh, Pennsylvania, 15213-4306, United States

  • Universitätsklinikum Frankfurt

    Frankfurt am Main, 60596, Germany

  • Universitätsklinikum Freiburg-Zentrum für Kinder- und Jugendmedizin

    Freiburg im Breisgau, 79106, Germany

  • Universitätsklinikum Hamburg-Eppendorf - University Medical Center Hamburg-Eppendorf

    Hamburg, 20246, Germany

  • Universitätsklinikum Regensburg

    Regensburg, 93053, Germany

  • VM Medical Park Mersin Hastanesi- Kardiyoloji

    Mersin, 33200, Turkey (Türkiye)

  • Versiti Blood Center of Wisconsin

    Milwaukee, Wisconsin, 53226, United States

  • Victoria Hospital, Bangalore

    Bangalore, 560002, India

  • Virginia Commonwealth University

    Richmond, Virginia, 23298, United States

  • Wake Forest Baptist Health

    Winston-Salem, North Carolina, 27157, United States

  • Washington University School of Medicine_St. Louis

    St Louis, Missouri, 63110, United States

  • Weill Cornell Med Coll-NYPH

    New York, New York, 10065, United States

  • Yale University

    New Haven, Connecticut, 06510, United States

  • Yashoda Hospital

    Hyderabad, Telangana, 500084, India

  • [Legal] Alexandria Clinical Research LLC

    Alexandria, 0, Egypt

  • [Legal] Alexandria Clinical Research LLC

    Alexandria, 21131, Egypt

  • [Legal] Baylor College of Medicine

    Houston, Texas, 77030, United States

  • [Legal] Children's Hospital Medical Center dba Cincinnati Children's

    Cincinnati, Ohio, 45229, United States

  • [Legal] Collaborative Neuroscience Network, LLC

    Long Beach, California, 90806, United States

  • [Legal] Dr. Vince Clinical Research, LLC and Dr. Vince Clinical Research, P.A.

    Detroit, Michigan, 48201, United States

  • [Legal] St. Jude Children's Research Hospital

    Memphis, Tennessee, 38105, United States

  • [Legal] The University of North Carolina at Chapel Hill

    Chapel Hill, North Carolina, 27514, United States

  • [Legal] Woodland International Research Group, LLC

    Little Rock, Arkansas, 72211, United States

  • iResearch Atlanta, LLC

    Decatur, Georgia, 30030, United States

  • Çukurova Üniversitesi Tıp Fakültesi Balcalı Hastanesi- Hematoloji

    Adana, 1130, Turkey (Türkiye)

Conditions

Explore the condition pages connected to this study.