New pill aims to boost blood health and cut pain crises in sickle cell
NCT ID NCT04624659
Summary
This study is testing whether a new oral medication called etavopivat can help people with sickle cell disease. It aims to increase healthy hemoglobin levels in the blood and reduce the frequency of painful vaso-occlusive crises. The trial involves 450 participants aged 12 to 65 and compares the medication against a placebo over a year of treatment.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for SICKLE CELL DISEASE are added.
By submitting, you agree to our Terms of use
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
By submitting, you agree to our Terms of use
Locations
-
'Ippokrateio' General Hospital of Thessaloniki
Thessaloniki, 54642, Greece
-
ARNAS Ospedali Civico Di Cristina Benfratelli - Presidio Ospedaliero "Civio e Benfratelli"
Palermo, 90127, Italy
-
Adana City Training and Research Hospital
Adana, 4522, Turkey (Türkiye)
-
Advanced Pharma CR
Miami, Florida, 33147, United States
-
Ain Shams University Hospital
Cairo, 1181, Egypt
-
Al Kasr AL Aini Hospital
Cairo, 11956, Egypt
-
All India Institute of Medical Sciences (AIIMS)
New Delhi, 110029, India
-
American University of Beirut Medical center
Beirut, 11-0236, Lebanon
-
Aminu Kano Teaching Hospital (AKTH)
Kano, 3452, Nigeria
-
Ap-Hp-Hopital Henri Mondor
Créteil, 94010, France
-
Ap-Hp-Hopital Robert Debre
Paris, 75019, France
-
Arnold Palmer Children's Hospital
Orlando, Florida, 32806, United States
-
Azienda Ospedale Universita Padova
Padua, 35128, Italy
-
Azienda Ospedaliera Universitaria San Luigi Gonzaga - S.C.D.O. Microcitemie e malattie rare ematologiche
Orbassano, 10043, Italy
-
Azienda Ospedaliero Universitaria Policlinico G. Rodolico - San Marco
Catania, 95123, Italy
-
Barau Dikko Teaching Hospital, Kaduna
Kaduna, 800212, Nigeria
-
Başkent Üniversitesi Adana Dr. Turgut Noyan Uygulama ve Araştırma Merkezi
Adana, 1240, Turkey (Türkiye)
-
Boston Medical Center
Boston, Massachusetts, 02118, United States
-
CHU Sainte-Justine Mother and Child University Hospital
Montreal, Quebec, H3T 1C5, Canada
-
Cairo University
Cairo, 111111, Egypt
-
Center for Blood Disorders Augusta University
Augusta, Georgia, 30912, United States
-
Centre Hospitalier Universitaire de Montpellier-Hopital Saint-Eloi
Montpellier, 34295, France
-
Centro per lo Studio e la Cura delle Amiloidosi Sistemiche Fondazione IRCCS Policlinico San Matteo
Pavia, PV, 27100, Italy
-
Charité - Campus Virchow-Klinikum - Klinik für Pädiatrie mit Schwerpunkt Onkologie und Hämatologie
Berlin, 13353, Germany
-
Children's Healthcare of Atlanta Investigational Medication Pharmacy
Atlanta, Georgia, 30342, United States
-
Children's Hosp-New Orleans
New Orleans, Louisiana, 70118, United States
-
Children's Hosptl Philadelphia
Philadelphia, Pennsylvania, 19104, United States
-
Children's National Health Hospital
Washington, New Jersey, 20010, United States
-
Churchill Hospital
Oxford, OX3 7LE, United Kingdom
-
Columbia University Medical Center_New York
New York, New York, 10032, United States
-
Complejo Hospitalario Universitario A Coruña
A Coruña, 15006, Spain
-
Cornerstone Research Institute
Altamonte Springs, Florida, 32701, United States
-
Duke University Medical Center
Durham, North Carolina, 27710, United States
-
East Carolina University
Greenville, North Carolina, 27858, United States
-
Ege Üniversitesi Tip Fakultesi Hastanesi - Nefroloji
Izmir, 35040, Turkey (Türkiye)
-
Emory University School of Medicine
Atlanta, Georgia, 30303, United States
-
Foundation for Sickle Cell Disease Research
Hollywood, Florida, 33023, United States
-
GHR Mulhouse Sud-Alsace
Mulhouse, 68100, France
-
Gen Hosp Athens Ippokrateio,B' Uni Clinic Internal Medicine
Athens, 115 27, Greece
-
General Hospital Of Larissa Koutlibaneio And Triantafylleio - Thalassemia and SCD Unit
Larissa, 41221, Greece
-
General University Hospital of Patras
Pátrai, Larissa, 265 04, Greece
-
Gertrude's Children's Hospital, Nairobi
Nairobi, 100, Kenya
-
Ghana Institute of Clinical Genetics, Korle Bu Teaching Hospital (KBTH)
Accra, 0, Ghana
-
Guys and St Thomas NHS Foundation Trust / Evelina Childrens Hospital
London, SE18 3RA, United Kingdom
-
Hacettepe Üniversitesi Hastanesi- Hematoloji
Ankara, 6230, Turkey (Türkiye)
-
Hammersmith Hospital - London
London, W2 1NY, United Kingdom
-
Hospices Civils de Lyon-Hopital Edouard Herriot
Lyon, 69437, France
-
Hospital Clinico San Carlos
Madrid, 28040, Spain
-
Hospital Germans Trias i Pujol
Badalona, 8916, Spain
-
Hospital Gregorio Marañón
Madrid, 28009, Spain
-
Hospital Nini
Tripoli, 113-6044, Lebanon
-
Hospital Ramón y Cajal
Madrid, 28034, Spain
-
Hospital Sant Joan de Déu
Barcelona, 8950, Spain
-
Hospital Universitario La Paz
Madrid, 28046, Spain
-
Hospital Universitario Virgen del Rocío
Seville, 41013, Spain
-
Hospital Universitario de Cruces
Barakaldo, 48903, Spain
-
Hospital Vall d'Hebron
Barcelona, 08035, Spain
-
Howard University
Washington D.C., District of Columbia, 20060, United States
-
Jacobi Medical Center
The Bronx, New York, 10461, United States
-
Jimmy Everest Cancer Hematology & Oncology
Oklahoma City, Oklahoma, 73104, United States
-
K.J Somaiya Hospital and Research Centre
Mumbai, Maharashtra, 400022, India
-
KEMRI Kondele Children Hospital, Kisumu
Kisumu, 40100, Kenya
-
KEMRI Siaya Clinical Research Annex Siaya County Referral Hospital, Siaya
Kisumu, 40600, Kenya
-
Karmanos Cancer Institute
Detroit, Michigan, 48201, United States
-
King Fahad Specialist Hospital-Dammam
Dammam, 32253, Saudi Arabia
-
King Khaled University Hospital,King Saud Univ. Med. City
Riyadh, 12372 6864, Saudi Arabia
-
Kings College Hospital - Haematology
London, SE5 9RS, United Kingdom
-
Kintampo Health Research Centre (KHRC), Kintampo, Ghana
Kintampo, 200, Ghana
-
Kombewa Clinical Research Centre
Kisumu, 1932, Kenya
-
Lagos University Teaching Hospital, Lagos
Lagos, 102215, Nigeria
-
Leicester Royal Infirmary - Haemostasis & Thrombosis Unit
Leicester, LE1 5WW, United Kingdom
-
Levine Cancer Institute
Charlotte, North Carolina, 28204, United States
-
Lynn Institute of Tulsa
Tulsa, Oklahoma, 74135, United States
-
Mary Bridge Children's Health
Tacoma, Washington, 98405, United States
-
Massachusetts General Hospital_Boston
Boston, Massachusetts, 02114, United States
-
Master Centre for Lebanon
Amman, 11844, Lebanon
-
Medical University of South Carolina
Charleston, South Carolina, 29425, United States
-
Mersin Üniversitesi Tip Fakültesi Hastanesi- Çiftlikköy Yerleşkesi- Hematoloji
Mersin, 33110, Turkey (Türkiye)
-
Methodist University Hospital
Memphis, Tennessee, 38104, United States
-
Montefiore Medical Center
The Bronx, New York, 10467, United States
-
NYC Health+Hospitals
Brooklyn, New York, 11203, United States
-
Neuro-Behavioral Clinical Research
North Canton, Ohio, 44720, United States
-
North Shore Long Island Jewish Medical Center
New Hyde Park, New York, 11040, United States
-
Ospedale Pediatrico Bambino Ges
Roma, 00165, Italy
-
Pacific Research Partners
Oakland, California, 94607, United States
-
Phoenix Children's Hsptl
Phoenix, Arizona, 85016, United States
-
Prince Mohammad Bin Naser Hospital
Jizan, 82943, Saudi Arabia
-
Prisma Health-Upstate
Greenville, South Carolina, 29605, United States
-
Providence Hematolgy
Vancouver, British Columbia, V6E 1M7, Canada
-
Queens Hospital Center
Jamaica, New York, 11432-1121, United States
-
Rhode Island Hospital
Providence, Rhode Island, 02903, United States
-
Royal Hallamshire Hospital
Sheffield, S11 8RN, United Kingdom
-
Saint-Denis Hospital Center
Saint-Denis, 93200, France
-
Sonar Clinical Research
Atlanta, Georgia, 30315, United States
-
Srirama Chandra Bhanj Medical College & Hospital (S.C.B Medical College)
Cutack, 753007, India
-
Sultan Qaboos University Hospital
Muscat, Sultanet of Oman/Muscat/Al Khoud, 123, Oman
-
Sydnawy University Hospital
Zagazig, 44519, Egypt
-
The Hospital for Sick Children
Toronto, Ontario, M5G 1X8, Canada
-
The Ohio State University Medical Center
Columbus, Ohio, 43203, United States
-
Thomas Jefferson University Hospital
Philadelphia, Pennsylvania, 19107, United States
-
UC Davis Medical Center
Sacramento, California, 95817, United States
-
UCSF Oakland Benioff ChildHosp
Oakland, California, 94609, United States
-
UT Health University of Texas
Houston, Texas, 77030, United States
-
Uniklinik Heidelberg - Klinik für Pädiatrische Onkologie, Hämatologie, Immunologie und Pneumologie
Heidelberg, 69120, Germany
-
Univ of Alabama Birmingham
Birmingham, Alabama, 35233, United States
-
University Health Network - Toronto General Hospital
Toronto, Ontario, M5G 2C4, Canada
-
University Hospital Lewisham, Lewisham and Greenwich NHS Trust
London, SE13 6LH, United Kingdom
-
University Of California Irvine
Orange, California, 92868, United States
-
University Of Maryland School of Medicine
Baltimore, Maryland, 21201, United States
-
University Of Miami
Miami, Florida, 33136, United States
-
University of Abuja Teaching Hospital, Gwagwalada, Abuja
Abuja, 228, Nigeria
-
University of Cincinnati
Cincinnati, Ohio, 45219, United States
-
University of Connecticut
Farmington, Connecticut, 06030, United States
-
University of Florida
Gainesville, Florida, 32610, United States
-
University of Illinois at Chicago
Chicago, Illinois, 60612, United States
-
University of Nebraska Medical Center
Omaha, Nebraska, 68198-2168, United States
-
University of Nigeria Teaching Hospital, Enugu
Lagos, 102215, Nigeria
-
University of Pittsburgh Medical Center
Pittsburgh, Pennsylvania, 15213-4306, United States
-
Universitätsklinikum Frankfurt
Frankfurt am Main, 60596, Germany
-
Universitätsklinikum Freiburg-Zentrum für Kinder- und Jugendmedizin
Freiburg im Breisgau, 79106, Germany
-
Universitätsklinikum Hamburg-Eppendorf - University Medical Center Hamburg-Eppendorf
Hamburg, 20246, Germany
-
Universitätsklinikum Regensburg
Regensburg, 93053, Germany
-
VM Medical Park Mersin Hastanesi- Kardiyoloji
Mersin, 33200, Turkey (Türkiye)
-
Versiti Blood Center of Wisconsin
Milwaukee, Wisconsin, 53226, United States
-
Victoria Hospital, Bangalore
Bangalore, 560002, India
-
Virginia Commonwealth University
Richmond, Virginia, 23298, United States
-
Wake Forest Baptist Health
Winston-Salem, North Carolina, 27157, United States
-
Washington University School of Medicine_St. Louis
St Louis, Missouri, 63110, United States
-
Weill Cornell Med Coll-NYPH
New York, New York, 10065, United States
-
Yale University
New Haven, Connecticut, 06510, United States
-
Yashoda Hospital
Hyderabad, Telangana, 500084, India
-
[Legal] Alexandria Clinical Research LLC
Alexandria, 0, Egypt
-
[Legal] Alexandria Clinical Research LLC
Alexandria, 21131, Egypt
-
[Legal] Baylor College of Medicine
Houston, Texas, 77030, United States
-
[Legal] Children's Hospital Medical Center dba Cincinnati Children's
Cincinnati, Ohio, 45229, United States
-
[Legal] Collaborative Neuroscience Network, LLC
Long Beach, California, 90806, United States
-
[Legal] Dr. Vince Clinical Research, LLC and Dr. Vince Clinical Research, P.A.
Detroit, Michigan, 48201, United States
-
[Legal] St. Jude Children's Research Hospital
Memphis, Tennessee, 38105, United States
-
[Legal] The University of North Carolina at Chapel Hill
Chapel Hill, North Carolina, 27514, United States
-
[Legal] Woodland International Research Group, LLC
Little Rock, Arkansas, 72211, United States
-
iResearch Atlanta, LLC
Decatur, Georgia, 30030, United States
-
Çukurova Üniversitesi Tıp Fakültesi Balcalı Hastanesi- Hematoloji
Adana, 1130, Turkey (Türkiye)
Conditions
Explore the condition pages connected to this study.