First human test of gene therapy for deadly heart rhythm disorder
NCT ID NCT07148089
Summary
This is an early safety study testing a single dose of an experimental gene therapy called SGT-501 in people with CPVT, a rare inherited condition that causes dangerous fast heart rhythms during exercise or stress. The main goal is to see if the treatment is safe and tolerable in a small group of adults and children. Participants will be closely monitored for five years after receiving the one-time infusion.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Boston Children's Hospital
RECRUITINGBoston, Massachusetts, 02459, United States
Contact Email: •••••@•••••
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Cleveland Clinic
RECRUITINGCleveland, Ohio, 44195, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Mayo Clinic
RECRUITINGRochester, Minnesota, 55905, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
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St. Paul's Hospital
RECRUITINGVancouver, British Columbia, BC V6Z 1Y6, Canada
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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University of Pennsylvania
NOT_YET_RECRUITINGPhiladelphia, Pennsylvania, 19104, United States
Conditions
Explore the condition pages connected to this study.