New hope for kids with rare, deadly lung disease
NCT ID NCT04175600
Summary
This study is testing whether adding a drug called selexipag to standard treatments can slow down the worsening of pulmonary arterial hypertension (PAH) in children aged 2 to 18. PAH is a rare, serious disease that causes high blood pressure in the lungs. The trial will compare selexipag against a placebo (inactive pill) to see if it helps delay serious health events like hospitalization or the need for a lung transplant.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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AOU Città della Salute e della Scienza di Torino, Presidio Ospedale Infantile Regina Margherita
Torino, 10126, Italy
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ASST Grande Ospedale Metropolitano Niguarda
Milan, 20162, Italy
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Azienda Ospedaliera Policlinico S. Orsola-Malpighi
Bologna, 40138, Italy
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Behcet Uz Pediatric Diseases and Surgery Training and Research Hospital
Izmir, 35210, Turkey (Türkiye)
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Beijing Anzhen Hospital
Beijing, 100029, China
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CAPA Istanbul University Medical Faculty
Istanbul, 34093, Turkey (Türkiye)
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CHU Arnaud de Villeneuve
Montpellier, 34295, France
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CICUM San Miguel
Guadalajara, 44160, Mexico
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Centre Hospitalier Universitaire Vaudois CHUV
Lausanne, 1011, Switzerland
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Chiang Mai University Hospital
Chiang Mai, 50200, Thailand
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Children's Hospital 1
Ho Chi Minh City, Vietnam
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Children's Hospital of Fudan University
Shanghai, 201102, China
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Children's National Medical Center
Washington D.C., District of Columbia, 20010, United States
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Childrens City Clinical Hospital n.a. Bashlyaeva
Moscow, 125373, Russia
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Childrens Hospital Colorado
Aurora, Colorado, 80045, United States
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Childrens Hospital Of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
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Chu Hopital Des Enfants
Toulouse, 31059, France
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Cincinnati Children's Hospital Medical Center
Cincinnati, Ohio, 45229, United States
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Clinica San Rafael
Bogotá, 0000000, Colombia
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Clínica Imbanaco S.A.S.
Cali, 760042, Colombia
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Complexo de Prevencao,Diagnostico,Terapia e Reabilitacao Respiratoria LTDA Hospital Dia do Pulmao
Blumenau, 89030-101, Brazil
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Congenital Heart Center of the University of Florida
Gainesville, Florida, 32610, United States
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Cukurova Balcali Hospital Application and Research Center
Adana, 01790, Turkey (Türkiye)
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Detroit Medical Center
Detroit, Michigan, 48201, United States
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Dnipropetrovsk clinical medical center of Mother and Child after prof. Rudnev
Dnipro, 49006, Ukraine
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Drottning Silvias barn- och ungdomssjukhus
Gothenburg, 416 50, Sweden
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Fundacao Universitaria de Cardiologia
Porto Alegre, 90620-001, Brazil
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Fundacao Universitaria de Cardiologia - Instituto de Cardiologia e Transplantes do DF
Brasília, 70310-500, Brazil
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Fundacion Cardiovascular de Colombia
Piedecuesta, 681017, Colombia
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Fundacion Neumologica Colombiana
Bogotá, 0000000, Colombia
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Fundacion Santa Fe de Bogota
Bogotá, Colombia
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Gottsegen György Országos Kardiológiai Intézet
Budapest, 1096, Hungary
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Guangzhou Women And Children's Medical Center
Guangzhou, 510623, China
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Hacettepe University Medical Faculty
Ankara, 06230, Turkey (Türkiye)
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Hanoi Medical University Hospital
Hanoi, Vietnam
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Health Institution 4Th City Children'S Clinical Hospital
Minsk, 220118, Belarus
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Herzzentrum Leipzig GmbH
Leipzig, 04289, Germany
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Hopital de la Timone
Marseille, 13385, France
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Hosp Univ A Coruna
A Coruña, 15006, Spain
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Hosp Univ Vall D Hebron
Barcelona, 08035, Spain
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Hosp. Gral. Univ. Gregorio Maranon
Madrid, 28009, Spain
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Hosp. Sant Joan de Deu
Esplugues de Llobregat, 08950, Spain
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Hosp. Univ. La Paz
Madrid, 28046, Spain
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Hosp. Virgen Del Rocio
Seville, 41013, Spain
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Hospital For Sick Children
Toronto, Ontario, M5G 1X8, Canada
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Hospital Pequeno Principe
Curitiba, 80250-060, Brazil
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Hospital Universidad del Norte
Soledad, 0000000, Colombia
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Hôpital Cardiologique - Chru Lille
Lille, 59037, France
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Hôpital Cardiologique Du Haut-Lévêque
Pessac, 33604, France
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Hôpital Necker - Enfants Malades
Paris, 75015, France
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IRCCS Policlinico San Donato
S. Donato Milanese, 20097, Italy
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Instytut Pomnik Centrum Zdrowia Dziecka
Warsaw, 04-730, Poland
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Irmandade Santa Casa de Misericordia de Porto Alegre
Porto Alegre, 90020-090, Brazil
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Irmandade Santa Casa de Misericordia de Sao Paulo
São Paulo, 01221-020, Brazil
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Izmir Tepecik Training and Research Hospital
Izmir, 35020, Turkey (Türkiye)
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Kaohsiung Veterans General Hospital
Kaohsiung City, 813414, Taiwan
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Kazan State Medical University
Kazan', 420012, Russia
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Kazan State Medical University 1
Kazan', 420059, Russia
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Klinikum der Universitaet Muenchen
München, 81377, Germany
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MI 'Dnipropetrovsk Regional Clinical Center of Cardiology and Cardiac Surgery'
Dnipro, 49070, Ukraine
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MI Zaporizhzhia Regional Clinical Childrens Hospital of Zaporizhzhia Regional Council
Zaporizhzhya, 69063, Ukraine
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Mehmet Akif Ersoy Training and Research Hospital
Istanbul, 34303, Turkey (Türkiye)
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Multiprofile Hospital For Active Treatment National Cardiology Hospital, Ead
Sofia, 1309, Bulgaria
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National Cheng Kung University Hospital
Tainan, 704, Taiwan
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National Heart Institute
Kuala Lumpur, 50400, Malaysia
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National Taiwan University Hospital
Taipei, 100, Taiwan
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New Children's Hospital of the Helsinki University Hospital (HUS)
Helsinki, 29, Finland
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Operadora de Hospitales Angeles SA de CV Hospital Angeles Lomas
México, 52787, Mexico
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Ospedale Pediatrico Bambin Gesù
Roma, 00193, Italy
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Our Lady's Children's Hospital
Dublin, Ireland
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Phoenix Children's Hospital
Phoenix, Arizona, 85016, United States
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Primary Children's Hospital
Salt Lake City, Utah, 84113, United States
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Pusan National University Yangsan Hospital
Yangsan, 50612, South Korea
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Qingdao Women and Children's Hospital
Qingdao, 266000, China
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Qingdao Women and Children's Hospital 1
Qingdao, 266000, China
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Queensland CHILDREN'S HOSPITAL
South Brisbane, 4101, Australia
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Rambam Medical Center
Haifa, 3109601, Israel
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Riley Hospital for Children
Indianapolis, Indiana, 46202, United States
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SPDM - Associacao Paulista para o Desenvolvimento da Medicina - Hospital Sao Paulo
São Paulo, 04024 002, Brazil
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Samara Regional Clinical Cardiological Dispensary
Samara, 443070, Russia
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Samsung Medical Center
Seoul, 06351, South Korea
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Scientific Practical Medical Center for Pediatric Cardiology and Cardio Surgery of the MOH
Kyiv, 04050, Ukraine
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Scientific and Research Institution of Cardiovascular Diseases Complex Problems
Kemerovo, 650002, Russia
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Secretaria da Saude do Estado do Ceara - Hospital Doutor Carlos Alberto Studart Gomes
Fortaleza, 60840-285, Brazil
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Seoul National University Hospital
Seoul, 03080, South Korea
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Severance Hospital Yonsei University Health System
Seoul, 120-752, South Korea
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Shanghai Childrens Medical Center
Shanghai, 200127, China
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Sheba Medical Center
Ramat Gan, 52621, Israel
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Skanes universitetssjukhus
Lund, 222 42, Sweden
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Slaskie Centrum Chorob Serca
Zabrze, 41-800, Poland
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Songklanagarind hospital
Songkhla, 90110, Thailand
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State Institution Republican Scientific And Practical Center For Pediatric Surgery
Minsk, 220013, Belarus
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Stollery Children's Hospital
Edmonton, Alberta, T6G 2B7, Canada
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Szpital Kliniczny im Karola Jonschera
Poznan, 60 572, Poland
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Tam Anh Hospital
Ho Chi Minh City, 700000, Vietnam
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Texas Children's Hospital
Houston, Texas, 77030, United States
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The General Hospital of Northern Theater Command
Shenyang, 110000, China
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UCLA Medical Center
Los Angeles, California, 90095, United States
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UCSF
San Francisco, California, 94158, United States
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ULB Hôpital Erasme
Brussels, 1070, Belgium
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Uls Sao Joao - Hosp. Sao Joao
Porto, 4200 319, Portugal
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Uls Sao Jose - Hosp. Santa Marta
Lisbon, 1169-024, Portugal
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Unidad de Investigacion Clinica en Medicina S.C. (UDICEM)
Monterrey, 64718, Mexico
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Universitaetsklinikum Heidelberg
Heidelberg, D-69120, Germany
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Universitair Ziekenhuis Gent
Ghent, 9000, Belgium
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Universitaire Ziekenhuizen Leuven
Leuven, 3000, Belgium
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University Medical Center Ho Chi Minh city
Ho Chi Minh City, 700000, Vietnam
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University of Virginia Division of Pediatric Cardiology
Charlottesville, Virginia, 22908, United States
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Universitätsklinikum Freiburg Zentrum
Freiburg im Breisgau, 70106, Germany
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Universta Degli Studi Di Padova
Padua, Italy
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Univerzitetska Dečja Klinika
Belgrade, 11000, Serbia
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Uniwersytecki Szpital Dzieciecy w Krakowie
Krakow, 30-663, Poland
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Uniwersyteckie Centrum Kliniczne
Gdansk, 80 952, Poland
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Veltischev Research and Clinical Institute for Pediatrics of the Pirogov RNRMU
Moscow, 125412, Russia
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Vilnius University Hospital Santariskiu Clinics
Vilnius, LT08661, Lithuania
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Wojewodzki Szpital Specjalistyczny we Wroclawiu
Wroclaw, 51 124, Poland
Conditions
Explore the condition pages connected to this study.