Could lower chemo save more babies with SCID? new study hopes to find out

NCT ID NCT03619551

First seen Oct 31, 2025 · Last updated May 15, 2026 · Updated 38 times

Summary

This study looks at whether using a lower dose of chemotherapy (busulfan) before a stem cell transplant can help babies with severe combined immunodeficiency (SCID) build a strong immune system with fewer side effects. About 56 infants with SCID will receive either a low or moderate dose of busulfan, followed by a transplant from an unrelated or half-matched donor. The goal is to see if they can make antibodies after vaccines, showing their immune system is working well.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • All Children's Hospital

    St. Petersburg, Florida, 33701, United States

  • Cancer Care Manitoba/University of Manitoba

    Winnipeg, Winnipeg, MB, Canada

  • Cardinal Glennon Children's Medical Center

    St Louis, Missouri, 63104, United States

  • Centre Hospitalier Universitaire Sainte-Justine

    Montreal, Montreal, QC, Canada

  • Children's Healthcare of Atlanta at Egleston

    Atlanta, Georgia, 30329, United States

  • Children's Hospital / LSUHSC

    New Orleans, Louisiana, 70118, United States

  • Children's Hospital Los Angeles

    Los Angeles, California, 90027, United States

  • Children's Hospital of Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

  • Children's Hospital of Pittsburgh of UPMC

    Pittsburgh, Pennsylvania, 15224, United States

  • Children's Hospital of Wisconsin

    Milwaukee, Wisconsin, 53226, United States

  • Children's Medical Center Dallas

    Dallas, Texas, 75235, United States

  • Children's National Medical Center

    Washington D.C., District of Columbia, 20010, United States

  • Cincinnati Children's Hospital Medical Center

    Cincinnati, Ohio, 45229, United States

  • Cleveland Clinic Foundation

    Cleveland, Ohio, 44195, United States

  • Cohen Children's Medical Center

    Queens, New York, 11040, United States

  • Comer Children's Hospital/University of Chicago Medicine

    Chicago, Illinois, 60637, United States

  • Dana Farber Cancer Institute - Peds

    Boston, Massachusetts, 02115, United States

  • Duke University Medical Center; Pediatric Blood and Marrow Transplant

    Durham, North Carolina, 27705, United States

  • Fred Hutchinson Cancer Research Center

    Seattle, Washington, 98109, United States

  • Hackensack University Medical Center

    Hackensack, New Jersey, 07601, United States

  • Helen DeVos Children's

    Grand Rapids, Michigan, 49503, United States

  • Indiana University Hospital/Riley Hospital for Children

    Indianapolis, Indiana, 46202, United States

  • Levine Children's Hospital

    Charlotte, North Carolina, 28203, United States

  • Mayo Clinic Arizona and Phoenix Children's Hospital

    Phoenix, Arizona, 85016, United States

  • Memorial Sloan Kettering Cancer Center - Peds

    New York, New York, 10065, United States

  • Morgan Stanley Children's Hospital of New York-Presbyterian - Columbia University Medical Center

    New York, New York, 10032, United States

  • Nebraska Medicine

    Omaha, Nebraska, 68198, United States

  • Oregon Health and Science University

    Portland, Oregon, 97239-3098, United States

  • Rady Children's Hospital, San Diego

    San Diego, California, 92123, United States

  • Shands HealthCare & University of Florida

    Gainesville, Florida, 32610, United States

  • The Children's Mercy Hospitals and Clinics

    Kansas City, Missouri, 64108, United States

  • The Hospital for Sick Children

    Toronto, Ontario, M5G 1E8, Canada

  • The University of Michigan

    Ann Arbor, Michigan, 48109, United States

  • UCLA Center for Health Sciences

    Los Angeles, California, 90095, United States

  • Univeristy of Alabama at Birmingham

    Birmingham, Alabama, 35294, United States

  • University of California San Francisco Medical Center - Peds

    San Francisco, California, 94143, United States

  • University of Colorado - Children's Hospital

    Aurora, Colorado, 80045, United States

  • University of Iowa Hospitals & Clinics

    Iowa City, Iowa, 52242, United States

  • University of Miami/Jackson Memorial Hospital

    Miami, Florida, 33136, United States

  • University of Minnesota Blood and Marrow Transplant Program - Pediatrics

    Minneapolis, Minnesota, 55455, United States

  • University of Wisconsin Hospital and Clinics

    Madison, Wisconsin, 53792, United States

  • Utah Blood and Marrow Transplant Program-Peds

    Salt Lake City, Utah, 84112, United States

  • Vanderbilt University Medical Center

    Nashville, Tennessee, 37232, United States

  • Westchester Medical Center

    Valhalla, New York, 10595, United States

Conditions

Explore the condition pages connected to this study.