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First patients to receive experimental drug for rare brain disease

NCT ID NCT06672445

Recruiting now Disease control Sponsor: Arrowhead Pharmaceuticals Source: ClinicalTrials.gov ↗

Summary

This early-stage trial is testing a new drug called ARO-ATXN2 in adults with spinocerebellar ataxia type 2 (SCA2), a rare genetic disorder that affects movement and coordination. The main goal is to check if the drug is safe and how it behaves in the body. Researchers will give a single dose to 36 participants (some receiving the drug, others a placebo) and monitor them closely.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Research Site 1

    RECRUITING

    Montreal, Quebec, H3A 2B4, Canada

  • Research Site 10

    RECRUITING

    Barcelona, 08035, Spain

  • Research Site 11

    RECRUITING

    Barcelona, 08036, Spain

  • Research Site 12

    RECRUITING

    Seville, 41013, Spain

  • Research Site 13

    RECRUITING

    Tübingen, Baden-Wurttemberg, 72026, Germany

  • Research Site 14

    RECRUITING

    Ulm, Baden-Wurttemberg, 89081, Germany

  • Research Site 15

    RECRUITING

    Paris, Paris, 75651, France

  • Research Site 16

    RECRUITING

    Milan, 20133, Italy

  • Research Site 2

    RECRUITING

    Montreal, Quebec, H2X 0C1, Canada

  • Research Site 3

    RECRUITING

    Christchurch, 8011, New Zealand

  • Research Site 4

    RECRUITING

    Auckland, 0622, New Zealand

  • Research Site 5

    RECRUITING

    Kaohsiung City, 833401, Taiwan

  • Research Site 6

    RECRUITING

    Taipei, 112201, Taiwan

  • Research Site 7

    RECRUITING

    Melbourne, Victoria, 3004, Australia

  • Research Site 8

    RECRUITING

    Sydney, New South Wales, 2170, Australia

  • Research Site 9

    RECRUITING

    Edmonton, 8440, Canada

Conditions

Explore the condition pages connected to this study.

SPINOCEREBELLAR ATAXIA TYPE 2