First-in-Human trial launches for rare brain disease treatment
NCT ID NCT06672445
Summary
This is an early-stage study to test the safety and body's response to a new drug called ARO-ATXN2 for adults with spinocerebellar ataxia type 2 (SCA2). Thirty-six participants will receive either a single dose of the drug or a placebo and be closely monitored. The main goal is to understand if the drug is safe and how it moves through and affects the body.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Research Site 1
RECRUITINGMontreal, Quebec, H3A 2B4, Canada
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Research Site 10
RECRUITINGBarcelona, 08035, Spain
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Research Site 11
RECRUITINGBarcelona, 08036, Spain
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Research Site 12
RECRUITINGSeville, 41013, Spain
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Research Site 13
RECRUITINGTübingen, Baden-Wurttemberg, 72026, Germany
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Research Site 14
RECRUITINGUlm, Baden-Wurttemberg, 89081, Germany
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Research Site 15
RECRUITINGParis, Paris, 75651, France
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Research Site 16
RECRUITINGMilan, 20133, Italy
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Research Site 2
RECRUITINGMontreal, Quebec, H2X 0C1, Canada
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Research Site 3
RECRUITINGChristchurch, 8011, New Zealand
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Research Site 4
RECRUITINGAuckland, 0622, New Zealand
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Research Site 5
RECRUITINGKaohsiung City, 833401, Taiwan
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Research Site 6
RECRUITINGTaipei, 112201, Taiwan
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Research Site 7
RECRUITINGMelbourne, Victoria, 3004, Australia
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Research Site 8
RECRUITINGSydney, New South Wales, 2170, Australia
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Research Site 9
RECRUITINGEdmonton, 8440, Canada
Conditions
Explore the condition pages connected to this study.