New hope for rare sugar disorder: experimental drug aims to slash dangerous lows

NCT ID NCT06208215

First seen Jan 09, 2026 · Last updated May 16, 2026 · Updated 17 times

Summary

This study tests an investigational drug called RZ358 in 56 people aged 3 months to 45 years with congenital hyperinsulinism, a rare condition causing dangerously low blood sugar. Participants receive RZ358 or a placebo added to their usual treatments for 24 weeks, followed by an open-label period where everyone can get RZ358. The goal is to see if RZ358 reduces hypoglycemia events and improves safety.

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Contacts and locations

Locations

  • Children's Hospital of Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

  • Cook Children's Medical Center

    Fort Worth, Texas, 76104, United States

  • Rezolute Investigative Site, Al Rayyan, Qatar

    Al Rayyan, Qatar

  • Rezolute Investigative Site, Ankara, Turkey

    Ankara, 06800, Turkey (Türkiye)

  • Rezolute Investigative Site, Athens, Greece

    Athens, 115 27, Greece

  • Rezolute Investigative Site, Barcelona, Spain

    Barcelona, 08035, Spain

  • Rezolute Investigative Site, Berlin, Germany

    Berlin, 13353, Germany

  • Rezolute Investigative Site, Bron, France

    Bron, 69677, France

  • Rezolute Investigative Site, Dusseldorf, Germany

    Düsseldorf, 40225, Germany

  • Rezolute Investigative Site, Hà Nội, Vietnam

    Hà Nội, 100000, Vietnam

  • Rezolute Investigative Site, London, United Kingdom

    London, WC1N 3JH, United Kingdom

  • Rezolute Investigative Site, Manchester, United Kingdom

    Manchester, M13 9WL, United Kingdom

  • Rezolute Investigative Site, Odense, Denmark

    Odense, 5000, Denmark

  • Rezolute Investigative Site, Paris, France

    Paris, 75015, France

  • Rezolute Investigative Site, Seeb, Oman

    Seeb, 123, Oman

  • Rezolute Investigative Site, Sevilla, Spain

    Seville, 41013, Spain

  • Rezolute Investigative Site, Tbilisi, Georgia

    Tbilisi, 0159, Georgia

  • Rezolute Investigative Site, Varna, Bulgaria

    Varna, 9010, Bulgaria

Conditions

Explore the condition pages connected to this study.