New hope for young patients with rare blood disorder

NCT ID NCT07001254

Summary

This study aims to see if adding the drug romiplostim to standard immunosuppressive therapy helps children and young adults (ages 2-21) with severe aplastic anemia. The goal is to improve their blood cell counts and reduce the need for transfusions. The main measure of success is whether patients achieve a complete blood count response after 24 weeks of treatment.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • University of Iowa Health Care

    Iowa City, Iowa, 52242, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.