New hope for kids with rare bone marrow failure: drug combo aims to restore blood cells

NCT ID NCT07001254

First seen Jan 05, 2026 · Last updated May 12, 2026 · Updated 16 times

Summary

This study tests whether adding romiplostim to standard immunosuppressive therapy helps children and young adults (ages 2–21) with severe aplastic anemia produce healthy blood cells. Participants have either newly diagnosed or hard-to-treat disease. The main goal is to see if blood counts improve without transfusions after 24 weeks.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • University of Iowa Health Care

    Iowa City, Iowa, 52242, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.