New study tracks Risdiplam's Real-World impact on spinal muscle atrophy

NCT ID NCT07531719

First seen Apr 24, 2026 · Last updated May 15, 2026 · Updated 6 times

Summary

This study follows 30 people with Type I or Type II spinal muscle atrophy who are starting or have started treatment with risdiplam. Researchers will track motor function improvements and safety over 24 months using standard tests. The goal is to see how well the drug works in everyday medical practice.

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