Gene therapy for rare blindness shows promise in Long-Term study
NCT ID NCT03406104
First seen Nov 01, 2025 · Last updated May 12, 2026 · Updated 27 times
Summary
This study followed 62 people with Leber Hereditary Optic Neuropathy (LHON) who received GS010 gene therapy in earlier trials. Researchers tracked eye safety and vision changes for up to 5 years after treatment. The goal was to see if the therapy remains safe and helps maintain or improve eyesight over time.
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This is a summary of
the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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CHNO Les Quinze Vingts
Paris, 75012, France
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Doheny Eye Center UCLA
Pasadena, California, 91105, United States
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Emory University Hospital
Atlanta, Georgia, 30322, United States
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LMU Klinikum der Universität München / Friedrich-Baur-Institut
Munich, 80336, Germany
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Moorfields Eye Hospital
London, Greater London, EC1V 2PD, United Kingdom
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Ospedale Bellaria
Bologna, 40139, Italy
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Wills Eye Institute
Philadelphia, Pennsylvania, 19107, United States
Conditions
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