New hope for rare disease patients as treatment study begins

NCT ID NCT05067868

Summary

This study aims to learn about the safety and effects of Replagal, an enzyme replacement therapy, in Indian children and adults with Fabry disease. Participants will receive Replagal infusions every two weeks at a clinic for about one year. The research will monitor side effects and check how the treatment affects kidney function, heart health, pain levels, and quality of life.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • All India Institute of Medical Sciences (AIIMS)

    RECRUITING

    New Delhi, 110029, India

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Institute of Child Health

    NOT_YET_RECRUITING

    Kolkata, 700017, India

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Sir Gangaram Hospital

    RECRUITING

    New Delhi, 110060, India

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.