FDA-Mandated 5-Year watch on new duchenne drug
NCT ID NCT07127978
Summary
This study will observe 300 patients with Duchenne muscular dystrophy (DMD) who are already taking the approved drug givinostat as part of their regular care. Researchers will track patients for up to 5 years to understand the drug's real-world safety, especially regarding low platelet counts and bleeding risks, and to see how it affects muscle function and daily life. No treatment is provided by the study; it simply collects data from routine doctor visits.
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Contacts and locations
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Locations
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Ann and Robert H. Lurie Children's Hospital of Chicago
RECRUITINGChicago, Illinois, 60611, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
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University of Massachusetts Chan Medical School
RECRUITINGWorcester, Massachusetts, 01655, United States
Contact Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
Conditions
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