New hope for rare blood disease: drug trial shows promise in controlling PNH

NCT ID NCT06578949

First seen Nov 18, 2025 · Last updated May 13, 2026 · Updated 18 times

Summary

This study tested a drug called ravulizumab in 18 adults in China with a rare blood disease called PNH, which destroys red blood cells. The goal was to see if the drug could lower a key blood marker of cell damage and reduce the need for blood transfusions. Participants received the drug intravenously and were monitored for 26 weeks.

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Contacts and locations

Locations

  • Research Site

    Beijing, CN-100730, China

  • Research Site

    Guangzhou, 510100, China

  • Research Site

    Hangzhou, 310003, China

  • Research Site

    Nantong, 226001, China

  • Research Site

    Shanghai, 200040, China

  • Research Site

    Tianjin, 300020, China

  • Research Site

    Tianjin, 300050, China

  • Research Site

    Wuhan, 430022, China

Conditions

Explore the condition pages connected to this study.