New hope for stem cell transplant patients facing deadly blood clot disorder
NCT ID NCT04543591
First seen Nov 01, 2025 · Last updated May 05, 2026 · Updated 30 times
Summary
This study tested a drug called ravulizumab in 148 people aged 12 and older who developed a serious blood clotting condition (thrombotic microangiopathy) after a stem cell transplant. The goal was to see if the drug could improve survival and prevent the condition from getting worse. Participants received either ravulizumab or a placebo along with standard care for 26 weeks, followed by 26 weeks of monitoring.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Tampa, Florida, 33612, United States
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Grosse Pointe Farms, Michigan, 48236, United States
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Durham, North Carolina, 27705, United States
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Pittsburgh, Pennsylvania, 15232, United States
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Seattle, Washington, 98109, United States
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Parkville, 3050, Australia
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Bruges, 8000, Belgium
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Brussels, 1200, Belgium
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Chênée, 4032, Belgium
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Yvoir, 5530, Belgium
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Cerqueira César, 05403-000, Brazil
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Florianópolis, 88034-000, Brazil
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Jaú, 17210-080, Brazil
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Porto Alegre, 90035-903, Brazil
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Porto Alegre, 90110-270, Brazil
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Rio de Janeiro, 20230-130, Brazil
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São José do Rio Preto, 15090-000, Brazil
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São Paulo, 05.403-010, Brazil
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Calgary, Alberta, T2N 4N1, Canada
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Suzhou, 215006, China
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Tianjin, 300020, China
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Angers, 49033, France
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La Tronche, 38043, France
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Nice, 06200, France
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Hamburg, 20246, Germany
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Ulm, 89081, Germany
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Athens, 12462, Greece
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Pátrai, 26504, Greece
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Thessaloniki, 57010, Greece
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Halfa, 31096, Israel
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Ramat Gan, 52621, Israel
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Roma, 00168, Italy
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Udine, 33100, Italy
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Akita, 010-8543, Japan
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Anjo, 446-8602, Japan
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Chiba, 260-8677, Japan
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Fukushima, 960-1295, Japan
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Isehara-shi, 259-1193, Japan
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Kurashiki-shi, 710-8602, Japan
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Minatoku, 105-8470, Japan
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Okayama, 700-8558, Japan
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Osaka, 545-8586, Japan
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Osakasayama-shi, 589-8511, Japan
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Sapporo, 060-8638, Japan
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Suita-shi, 565-0871, Japan
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Tsukuba, 305-8576, Japan
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Wakayama, 641-8510, Japan
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Groningen, 9713 GZ, Netherlands
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Goyang-si, 10408, South Korea
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Seoul, 03080, South Korea
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Seoul, 03722, South Korea
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Seoul, 06351, South Korea
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Barcelona, 08036, Spain
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Granada, 18014, Spain
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L'Hospitalet de Llobregat, 08908, Spain
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Madrid, 28007, Spain
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Madrid, 28034, Spain
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Madrid, 28040, Spain
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Madrid, 28046, Spain
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Málaga, 29010, Spain
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Pamplona, 31008, Spain
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Salamanca, 37007, Spain
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Seville, 41013, Spain
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Huddinge, 141 57, Sweden
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London, W12 0HS, United Kingdom
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Nottingham, NG5 1PB, United Kingdom
Conditions
Explore the condition pages connected to this study.