Scientists gather clues about Ultra-Rare metabolic disorders

NCT ID NCT06795152

Summary

This study aims to collect medical information from people with several ultra-rare glycogen storage diseases (GSDs) to better understand how these conditions progress over time. Researchers will review medical records from about 200 participants to create a detailed database of symptoms, test results, and health outcomes. The information gathered will help doctors describe these rare diseases more accurately and could guide the development of future treatments.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Duke University

    RECRUITING

    Durham, North Carolina, 27710, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.