Hope for rare brain disorder: new drug trial targets seizures and symptoms

NCT ID NCT07224581

First seen Nov 05, 2025 · Last updated May 15, 2026 · Updated 22 times

Summary

This study tests an experimental drug called radiprodil in people with a rare genetic brain condition called GRIN-related neurodevelopmental disorder. The trial includes two groups: one with frequent seizures and one with other symptoms but fewer seizures. Participants will either receive the drug or a placebo for 16-28 weeks, then all can receive the drug in an open-label extension. The goal is to see if radiprodil reduces seizures and improves daily symptoms safely.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Boston Children's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

  • Child Neurology Consultants of Austin - South Austin

    RECRUITING

    Austin, Texas, 78757, United States

  • Children's Hospital Colorado - Anschutz Medical Campus

    RECRUITING

    Aurora, Colorado, 80045, United States

  • Children's Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

  • Children's National Hospital

    RECRUITING

    Washington D.C., District of Columbia, 20010, United States

  • Cincinnati Children's Hospital Medical Center

    NOT_YET_RECRUITING

    Cincinnati, Ohio, 45229, United States

  • Columbia University - Harkness

    RECRUITING

    New York, New York, 10032, United States

  • Duke Health-Duke Children's Hospital & Health Center

    RECRUITING

    Durham, North Carolina, 27705, United States

  • Iowa Health Care - Pediatric Neurology & Specialty Clinic

    RECRUITING

    Iowa City, Iowa, 52242, United States

  • Lucile Packard Children's Hospital

    RECRUITING

    Palo Alto, California, 94304, United States

  • Nicklaus Children's Hospital

    RECRUITING

    Miami, Florida, 33155, United States

  • Northeast Regional Epilepsy Group (NEREG) - Hackensack

    RECRUITING

    Hackensack, New Jersey, 07601, United States

  • Pediatric Neurology and Epilepsy

    RECRUITING

    Winter Park, Florida, 32789, United States

  • Seattle Children's Hospital

    RECRUITING

    Seattle, Washington, 98105, United States

  • The University of Texas Southwestern Medical Center (UTSW)

    NOT_YET_RECRUITING

    Dallas, Texas, 75390, United States

  • UCLA Clinical & Translational Research Center

    RECRUITING

    Los Angeles, California, 90095, United States

  • UTHealth Houston

    RECRUITING

    Houston, Texas, 77030, United States

Conditions

Explore the condition pages connected to this study.