First human trial for genetic eye disease treatment begins

NCT ID NCT06970106

Summary

This early-stage study is testing the safety of a new eye injection called PYC-001 in adults with a specific genetic condition that causes progressive vision loss (OPA1-related optic atrophy). About 21 participants in the UK and Australia will receive different doses and schedules of the injection to find the safest and most suitable regimen. The main goal is to see how well the treatment is tolerated and to gather initial data on its effect on eye structure and vision.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Cerulea Clinical Trials

    RECRUITING

    East Melbourne, Australia

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Retina Specialists

    RECRUITING

    Auckland, 1052, New Zealand

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Save Sight Institute - Sydney Eye Hospital

    RECRUITING

    Sydney, New South Wales, 2000, Australia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.