New hope for kids with devastating brain cancer: first safety trial of experimental drug

NCT ID NCT03605550

Summary

This study is testing the safety of a new oral drug called PTC596 (Unesbulin) when given alongside standard radiation therapy to children and young adults newly diagnosed with aggressive brain tumors, including a very hard-to-treat type called DIPG. The main goals are to find the safest dose and see how much of the drug gets into the blood and, for some patients, the tumor itself. This is an early-phase trial focused on safety and dosing, not proving the drug's effectiveness.

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Contacts and locations

Locations

  • Ann & Robert H. Lurie Children's Hospital of Chicago

    Chicago, Illinois, 60611, United States

  • Children's Hospital Colorado

    Aurora, Colorado, 80045, United States

  • Children's National Medical Center

    Washington D.C., District of Columbia, 20010, United States

  • Cincinnati Children's Hospital Medical Center

    Cincinnati, Ohio, 45229, United States

  • Dana-Farber Cancer Institute

    Boston, Massachusetts, 02215, United States

  • Duke University Medical Center

    Durham, North Carolina, 27710, United States

  • Nationwide Children's Hospital

    Columbus, Ohio, 43205, United States

  • Seattle Children's Hospital

    Seattle, Washington, 98105, United States

  • Texas Children's Hospital

    Houston, Texas, 77030, United States

  • The Children's Hospital of Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

Conditions

Explore the condition pages connected to this study.