New pill shows promise for boosting growth in kids with dwarfism
NCT ID NCT04265651
First seen Nov 01, 2025 · Last updated May 17, 2026 · Updated 29 times
Summary
This study tested an oral medication called infigratinib in 84 children aged 3 to 11 with achondroplasia, the most common form of dwarfism. The drug aims to improve growth by targeting a specific protein linked to the condition. Researchers measured safety, side effects, and how much children grew over time.
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This is a summary of
the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Birmingham Children's Hospital
Birmingham, United Kingdom
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Cincinnati Children's Hospital Medical Center
Cincinnati, Ohio, 45229, United States
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Evelina London Children's Hospital
London, United Kingdom
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Hopital Femme Mere Enfant
Lyon, France
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Hopital Necker-Enfants Malades
Paris, France
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Hopital des Enfants
Toulouse, France
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Hospital Universitario La Paz
Madrid, 24086, Spain
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Hospital Universitario Virgen de la Victoria
Málaga, Spain
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Johns Hopkins School of Medicine
Baltimore, Maryland, 21211, United States
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Manchester University Children's Hospital
Manchester, United Kingdom
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Murdoch Children's Hospital
Parkville, Victoria, 3052, Australia
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Nemours Alfred I. Dupont Hospital for Children
Wilmington, Delaware, 19803, United States
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Queen Elizabeth University Hospital
Glasgow, United Kingdom
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Sheffield Children's Hospital
Sheffield, England, S10 2TH, United Kingdom
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Stollery Children's Hospital
Edmonton, Alberta, T6G 2H7, Canada
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UCSF Benioff Children's Hospital
Oakland, California, 94618, United States
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University Hospitals Bristol and Weston NHS Foundation Trust
Bristol, BS1 3NU, United Kingdom
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Vanderbilt University Medical Center
Nashville, Tennessee, 37232, United States
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Vithas Hospital San José
Vitoria-Gasteiz, Álava, 01012, Spain
Conditions
Explore the condition pages connected to this study.