New hope for kids with CF: triple therapy shows promise in young patients

NCT ID NCT04613128

First seen Nov 03, 2025 · Last updated May 14, 2026 · Updated 32 times

Summary

This study looked at how well a triple combination therapy (elexacaftor, tezacaftor, and ivacaftor, or ETI) works in children aged 6 to 11 with cystic fibrosis (CF) who have a specific genetic mutation. Researchers measured changes in sweat chloride, lung function, and growth over 24 months. The goal was to understand the therapy's real-world benefits and collect data for future research.

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Contacts and locations

Locations

  • Ann & Robert H. Lurie Children's Hospital of Chicago

    Chicago, Illinois, 60611, United States

  • Baylor College of Medicine

    Houston, Texas, 77030, United States

  • Boston Children's Hospital, Brigham & Women's Hospital

    Boston, Massachusetts, 02115, United States

  • Children's Hospital Colorado

    Aurora, Colorado, 80045, United States

  • Children's Hospital of Wisconsin

    Milwaukee, Wisconsin, 53226, United States

  • Children's Mercy Kansas City

    Kansas City, Missouri, 64108, United States

  • Cincinnati Children's Hospital Medical Center

    Cincinnati, Ohio, 45229, United States

  • John Hopkins University

    Baltimore, Maryland, 21287, United States

  • Oregon Health Sciences University

    Portland, Oregon, 97239, United States

  • Rainbow Babies and Children's Hospital/University Hospitals Cleveland Medical Center

    Cleveland, Ohio, 44146, United States

  • Riley Hospital for Children

    Indianapolis, Indiana, 46202, United States

  • Seattle Children's Hospital

    Seattle, Washington, 98105, United States

  • Stanford University Medical Center

    Palo Alto, California, 94304, United States

  • The Minnesota Cystic Fibrosis Center

    Minneapolis, Minnesota, 55455, United States

  • University of Alabama at Birmingham

    Birmingham, Alabama, 35294, United States

  • University of Iowa

    Iowa City, Iowa, 52242, United States

  • University of North Carolina at Chapel Hill

    Chapel Hill, North Carolina, 27599, United States

  • University of Wisconsin

    Madison, Wisconsin, 53792, United States

  • Virginia Commonwealth University

    Richmond, Virginia, 23219, United States

  • Washington University School of Medicine

    St Louis, Missouri, 63110, United States

Conditions

Explore the condition pages connected to this study.