First major study to track babies exposed to rare disease drug in the womb

NCT ID NCT05579548

Summary

This study aims to gather safety information on the PKU drug Palynziq (pegvaliase) when used during pregnancy and breastfeeding. Researchers will follow about 50 pregnant women with PKU who are already taking the drug and track the health of both the mothers and their babies for about 21 months. The goal is to understand if the medication affects pregnancy outcomes or infant development.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for PHENYLKETONURIA, MATERNAL are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Metabolics and Genetics in Calgary (MAGIC)

    RECRUITING

    Calgary, T2E 7Z4, Canada

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Ospedale San Paolo

    RECRUITING

    Milan, 20142, Italy

    Contact Email: •••••@•••••

  • Syneos Health

    RECRUITING

    Wilmington, North Carolina, 28403, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Universitaetsklinikum Hamburg Eppendorf

    RECRUITING

    Hamburg, 20246, Germany

    Contact Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.