Global effort launched to map rare muscle disease

NCT ID NCT00231400

Recruiting now Knowledge-focused Sponsor: Genzyme, a Sanofi Company Source: ClinicalTrials.gov ↗

Summary

This global registry aims to better understand Pompe disease, a rare genetic disorder that causes muscle weakness. It will track 2,000 patients over time, both those receiving treatment and those who are not, to learn how the disease progresses and how treatments work long-term. The information collected will help doctors improve care and guide future research.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

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Study contacts

Contact

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Contact

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Locations

Ann and Robert Lurie Children's Hospital- Site Number : 840011
RECRUITING

Chicago, Illinois, 60611, United States
Ann and Robert Lurie Children's Hospital- Site Number : 840013
RECRUITING

Chicago, Illinois, 60611, United States
Arkansas Childrens Hospital- Site Number : 840109
RECRUITING

Little Rock, Arkansas, 72202, United States
Atlantic Health System- Site Number : 840099
RECRUITING

Morristown, New Jersey, 07962, United States
Barrow Neurological Institute- Site Number : 840087
RECRUITING

Phoenix, Arizona, 85013, United States
Baylor Research Center- Site Number : 840058
RECRUITING

Dallas, Texas, 75226, United States
Baystate Health- Site Number : 840002
RECRUITING

Springfield, Massachusetts, 01199, United States
Boston Children's Hospital - PIN- Site Number : 840092
RECRUITING

Boston, Massachusetts, 02115, United States
Carolinas Medical Center Hospital- Site Number : 840065
RECRUITING

Charlotte, North Carolina, 28232, United States
Children's Hospital Colorado - Aurora- Site Number : 840069
COMPLETED

Aurora, Colorado, 80045, United States
Children's Hospital Oakland- Site Number : 840029
COMPLETED

Oakland, California, 94609, United States
Children's Hospital and Clinics of Minnesota- Site Number : 840046
COMPLETED

Minneapolis, Minnesota, 55404, United States
Children's Hospital of Michigan- Site Number : 840066
RECRUITING

Detroit, Michigan, 48201, United States
Children's Hospital of Orange County- Site Number : 840074
RECRUITING

Orange, California, 92868, United States
Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089
RECRUITING

Philadelphia, Pennsylvania, 19104, United States
Children's Hospital of Philadelphia- Site Number : 840034
RECRUITING

Philadelphia, Pennsylvania, 19104, United States
Children's Hospital of Wisconsin-Pediatrics- Site Number : 840054
RECRUITING

Milwaukee, Wisconsin, 53226, United States
Children's Hospital of the Kings Daughters- Site Number : 840072
COMPLETED

Norfolk, Virginia, 23507, United States
Children's Hospitals and Clinics of Minnesota- Site Number : 840114
RECRUITING

Minneapolis, Minnesota, 55404, United States
Children's Mercy Hospital- Pediatrics- Site Number : 840063
COMPLETED

Kansas City, Missouri, 64108, United States
Children's National Medical Center- Site Number : 840067
RECRUITING

Washington D.C., District of Columbia, 20010, United States
Children's Specialty Center of Nevada- Site Number : 840008
RECRUITING

Las Vegas, Nevada, 89109, United States
Cincinnati Children's Hospital-Genetics- Site Number : 840041
RECRUITING

Cincinnati, Ohio, 45229, United States
Cleveland Clinic Foundation Pediatrics- Site Number : 840048
RECRUITING

Cleveland, Ohio, 44195, United States
Cook Children's Health Care System- Site Number : 840024
RECRUITING

Fort Worth, Texas, 76104, United States
Cooper Health Center- Site Number : 840098
TERMINATED

Camden, New Jersey, 08103, United States
Duke University Medical Center Genetics Dept- Site Number : 840037
RECRUITING

Durham, North Carolina, 27710, United States
Emory University School of Medicine- Human Genetics- Site Number : 840060
RECRUITING

Decatur, Georgia, 30033, United States
Greenwood Genetcs- Site Number : 840055
RECRUITING

Greenville, South Carolina, 29605, United States
Hackensack University Medical Center- Site Number : 840101
RECRUITING

Hackensack, New Jersey, 07601, United States
Hospital Geral e Maternidade de Cuiabá- Site Number : 076003
RECRUITING

Cuiabá, Mato Grosso, 78025-000, Brazil
Hospital Universitario Walter Cantidio- Site Number : 076011
COMPLETED

Fortaleza, Ceará, 60430-270, Brazil
Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo- Site Number : 076004
RECRUITING

São Paulo, 05403-000, Brazil
Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo- Site Number : 076007
RECRUITING

São Paulo, 05403-000, Brazil
Hospital das Clinicas da Faculdade de Medicina de Ribeirao Preto- Site Number : 076009
RECRUITING

Ribeirão Preto, São Paulo, 14049-900, Brazil
Hospital de Clinicas de Porto Alegre- Site Number : 076008
RECRUITING

Porto Alegre, Rio Grande do Sul, 90035-903, Brazil
Indianapolis University School of Medicine- Site Number : 840027
RECRUITING

Indianapolis, Indiana, 46202, United States
Infusion Associates- Site Number : 840050
RECRUITING

Grand Rapids, Michigan, 49525, United States
Instituto Fernandes Figueira - FIOCRUZ- Site Number : 076001
RECRUITING

Rio de Janeiro, 22250020, Brazil
Instituto de Genética e Erros Inatos do Metabolismo- Site Number : 076002
RECRUITING

São Paulo, 04020-041, Brazil
Investigational Site Number : 036013
RECRUITING

Westmead, New South Wales, 2145, Australia
Investigational Site Number : 056010
RECRUITING

Brussels, 1200, Belgium
Investigational Site Number : 100001
RECRUITING

Sofia, 1680, Bulgaria
Investigational Site Number : 124001
RECRUITING

Sherbrooke, Quebec, J1H5N4, Canada
Investigational Site Number : 124002
RECRUITING

Edmonton, Alberta, TG62B7, Canada
Investigational Site Number : 124004
RECRUITING

Montreal, Quebec, H3A2B4, Canada
Investigational Site Number : 124006
RECRUITING

Toronto, Ontario, M5G 1X8, Canada
Investigational Site Number : 124007
RECRUITING

Hamilton, Ontario, L8N3Z5, Canada
Investigational Site Number : 124010
RECRUITING

Vancouver, British Columbia, V5Z1M9, Canada
Investigational Site Number : 124011
COMPLETED

Vancouver, British Columbia, V6H3N1, Canada
Investigational Site Number : 124014
RECRUITING

Calgary, Alberta, T2E 7Z4, Canada
Investigational Site Number : 124018
RECRUITING

Montreal, Quebec, H4A3J1, Canada
Investigational Site Number : 124019
RECRUITING

Winnipeg, Manitoba, R3A1R9, Canada
Investigational Site Number : 124021
RECRUITING

London, Ontario, N6A 5W9, Canada
Investigational Site Number : 124022
RECRUITING

Moncton, New Brunswick, E1C 2Z3, Canada
Investigational Site Number : 150031
RECRUITING

Mainz, 55131, Germany
Investigational Site Number : 150303
RECRUITING

London, WC1N 3JH, United Kingdom
Investigational Site Number : 150455
RECRUITING

Manchester, M8 5RB, United Kingdom
Investigational Site Number : 150575
RECRUITING

Warsaw, 04-730, Poland
Investigational Site Number : 150684
COMPLETED

Brussels, 1070, Belgium
Investigational Site Number : 150722
RECRUITING

Antwerp, 2020, Belgium
Investigational Site Number : 150809
RECRUITING

Prague, 12808, Czechia
Investigational Site Number : 150964
RECRUITING

Salford, Manchester, M6 8HD, United Kingdom
Investigational Site Number : 151015
RECRUITING

Murdoch, Western Australia, 6150, Australia
Investigational Site Number : 151069
RECRUITING

Westmead, New South Wales, 2145, Australia
Investigational Site Number : 151123
RECRUITING

London, NW32QG, United Kingdom
Investigational Site Number : 151149
RECRUITING

Seoul, 05505, South Korea
Investigational Site Number : 151179
RECRUITING

Taichung, 404, Taiwan
Investigational Site Number : 151181
RECRUITING

Taichung, 00407, Taiwan
Investigational Site Number : 151182
RECRUITING

Taipei, 100, Taiwan
Investigational Site Number : 151229
RECRUITING

København Ø, 2100, Denmark
Investigational Site Number : 151340
RECRUITING

Cambridge, Cambridgeshire, CB2 2QQ, United Kingdom
Investigational Site Number : 151500
RECRUITING

Chiayi City, Taiwan
Investigational Site Number : 151534
RECRUITING

New Taipei City, 23142, Taiwan
Investigational Site Number : 151646
RECRUITING

London, WC1N 3BG, United Kingdom
Investigational Site Number : 151668
RECRUITING

Leuven, 3000, Belgium
Investigational Site Number : 151686
RECRUITING

Berlin, 13353, Germany
Investigational Site Number : 152001
RECRUITING

Santiago, Chile
Investigational Site Number : 152002
COMPLETED

Punta Arenas, Chile
Investigational Site Number : 152029
RECRUITING

Rotterdam, 3015 CE, Netherlands
Investigational Site Number : 152041
COMPLETED

Berlin, 13125, Germany
Investigational Site Number : 152045
RECRUITING

Halle, 06120, Germany
Investigational Site Number : 152072
RECRUITING

Edegem, 2650, Belgium
Investigational Site Number : 152075
RECRUITING

München, 80336, Germany
Investigational Site Number : 152087
RECRUITING

Newcastle, NE13BZ, United Kingdom
Investigational Site Number : 152096
TERMINATED

Brisbane, Queensland, 4101, Australia
Investigational Site Number : 152108
RECRUITING

Freiburg im Breisgau, 79106, Germany
Investigational Site Number : 152126
RECRUITING

Leuven, 3000, Belgium
Investigational Site Number : 152152
RECRUITING

Hualien City, 970, Taiwan
Investigational Site Number : 152153
RECRUITING

Tainan, 710, Taiwan
Investigational Site Number : 152156
RECRUITING

Glasgow, G514TF, United Kingdom
Investigational Site Number : 152200
RECRUITING

Bonn, 53127, Germany
Investigational Site Number : 152218
RECRUITING

CABA, Buenos Aires, 1424, Argentina
Investigational Site Number : 152226
RECRUITING

Taipei, 112, Taiwan
Investigational Site Number : 152234
RECRUITING

Bochum, 44789, Germany
Investigational Site Number : 152244
RECRUITING

Kaohsiung City, 807, Taiwan
Investigational Site Number : 152246
RECRUITING

Kaohsiung City, 833, Taiwan
Investigational Site Number : 152287
RECRUITING

Birmingham, B15 2TH, United Kingdom
Investigational Site Number : 152293
RECRUITING

Berlin, 13353, Germany
Investigational Site Number : 152295
RECRUITING

Ghent, 9000, Belgium
Investigational Site Number : 152299
COMPLETED

Münster, 48149, Germany
Investigational Site Number : 152321
RECRUITING

Taipei, 10449, Taiwan
Investigational Site Number : 152334
RECRUITING

Cardiff, Cardiff [Caerdydd Gb-crd], CF14 4XW, United Kingdom
Investigational Site Number : 152356
TERMINATED

Shanghai, 200092, China
Investigational Site Number : 152379
TERMINATED

Guangzhou, 510000, China
Investigational Site Number : 152380
TERMINATED

Beijing, China
Investigational Site Number : 152381
TERMINATED

Jinan, 250014, China
Investigational Site Number : 152382
TERMINATED

Shanghai, China
Investigational Site Number : 153032
COMPLETED

Ciudad Autónoma de Buenos Aires, Buenos Aires, 1425, Argentina
Investigational Site Number : 153158
RECRUITING

Tao Yuan County, 333, Taiwan
Investigational Site Number : 153176
RECRUITING

Seoul, Seoul-teukbyeolsi, 06273, South Korea
Investigational Site Number : 153178
COMPLETED

Yangsan, Gyeongsangnam-do, 50612, South Korea
Investigational Site Number : 153179
RECRUITING

Gosselies, 6041, Belgium
Investigational Site Number : 153180
RECRUITING

Seoul, Seoul-teukbyeolsi, 03080, South Korea
Investigational Site Number : 153191
RECRUITING

Daejeon, South Korea
Investigational Site Number : 153192
COMPLETED

Seoul, 04401, South Korea
Investigational Site Number : 153194
ACTIVE_NOT_RECRUITING

CABA, Buenos Aires, CPC1181ACH, Argentina
Investigational Site Number : 153195
RECRUITING

Caba, Buenos Aires, Buenos Aires, C1415EKV, Argentina
Investigational Site Number : 153196
COMPLETED

Seoul, Seoul-teukbyeolsi, 03080, South Korea
Investigational Site Number : 153202
TERMINATED

Beijing, China
Investigational Site Number : 153203
COMPLETED

Beijing, China
Investigational Site Number : 153212
RECRUITING

Seoul, South Korea
Investigational Site Number : 153222
RECRUITING

Seoul, South Korea
Investigational Site Number : 153248
RECRUITING

Tainan, 704, Taiwan
Investigational Site Number : 154087
COMPLETED

Brisbane, Queensland, 4029, Australia
Investigational Site Number : 154093
RECRUITING

Chiayi City, Taiwan
Investigational Site Number : 154099
RECRUITING

Bucharest, 022328, Romania
Investigational Site Number : 154150
RECRUITING

Giessen, 35392, Germany
Investigational Site Number : 154212
RECRUITING

Hanoi, Vietnam
Investigational Site Number : 154215
RECRUITING

Hamburg, 20354, Germany
Investigational Site Number : 154225
COMPLETED

Kuwait City, Kuwait
Investigational Site Number : 154240
RECRUITING

Birmingham, B46NH, United Kingdom
Investigational Site Number : 154264
RECRUITING

Karachi, Pakistan
Investigational Site Number : 154266
RECRUITING

Lahore, Pakistan
Investigational Site Number : 154298
RECRUITING

Bruges, 8000, Belgium
Investigational Site Number : 157218
RECRUITING

Pisa, 56126, Italy
Investigational Site Number : 157250
RECRUITING

Jinan, 250014, China
Investigational Site Number : 170001
RECRUITING

Bogotá, Colombia
Investigational Site Number : 1910001
RECRUITING

Zagreb, 10000, Croatia
Investigational Site Number : 1910002
RECRUITING

Zagreb, 10000, Croatia
Investigational Site Number : 250001
RECRUITING

Paris, 75651, France
Investigational Site Number : 250002
COMPLETED

Marseille, 13385, France
Investigational Site Number : 250003
RECRUITING

Bron, 69677, France
Investigational Site Number : 250004
RECRUITING

Paris, 75015, France
Investigational Site Number : 250005
RECRUITING

Nice, 06001, France
Investigational Site Number : 250006
RECRUITING

Tours, 37032, France
Investigational Site Number : 250007
RECRUITING

Bron, 69677, France
Investigational Site Number : 250008
RECRUITING

Lille, 59037, France
Investigational Site Number : 250009
RECRUITING

Caen, 14033, France
Investigational Site Number : 250010
COMPLETED

Bordeaux, 33076, France
Investigational Site Number : 250011
RECRUITING

Nîmes, 30029, France
Investigational Site Number : 250012
RECRUITING

Brest, 29200, France
Investigational Site Number : 250014
RECRUITING

Toulouse, 31059, France
Investigational Site Number : 250015
RECRUITING

La Tronche, 38700, France
Investigational Site Number : 250016
RECRUITING

Strasbourg, 67200, France
Investigational Site Number : 250017
RECRUITING

Nancy, 54035, France
Investigational Site Number : 250018
RECRUITING

Saint-Priest-en-Jarez, 42270, France
Investigational Site Number : 250019
RECRUITING

Nantes, 44093, France
Investigational Site Number : 25013
RECRUITING

Vannes, 56017, France
Investigational Site Number : 300001
RECRUITING

Thessaloniki, 546 42, Greece
Investigational Site Number : 344001
RECRUITING

Kowloon, Hong Kong
Investigational Site Number : 3480007
RECRUITING

Nyíregyháza, 4400, Hungary
Investigational Site Number : 3480009
RECRUITING

Debrecen, 4032, Hungary
Investigational Site Number : 3480011
RECRUITING

Pécs, 7623, Hungary
Investigational Site Number : 3560004
RECRUITING

Secunderabad, 500026, India
Investigational Site Number : 356001
RECRUITING

Kolkata, 700017, India
Investigational Site Number : 356002
RECRUITING

Vellore, 632004, India
Investigational Site Number : 356003
RECRUITING

Ahmedabad, 380015, India
Investigational Site Number : 360001
RECRUITING

Jakarta, Indonesia
Investigational Site Number : 3760001
RECRUITING

Haifa, Israel
Investigational Site Number : 3760002
RECRUITING

Beersheba, Israel
Investigational Site Number : 3760003
COMPLETED

Tel Aviv, Israel
Investigational Site Number : 380001
RECRUITING

Udine, 33100, Italy
Investigational Site Number : 380002
RECRUITING

Padua, 35128, Italy
Investigational Site Number : 380003
RECRUITING

Pavia, 27100, Italy
Investigational Site Number : 380004
RECRUITING

Genova, 16147, Italy
Investigational Site Number : 380005
RECRUITING

Florence, 50141, Italy
Investigational Site Number : 380006
RECRUITING

Cagliari, 09126, Italy
Investigational Site Number : 380007
RECRUITING

Milan, Milano, 20133, Italy
Investigational Site Number : 380008
RECRUITING

Brescia, 25123, Italy
Investigational Site Number : 380009
RECRUITING

Monza, Italy
Investigational Site Number : 380010
RECRUITING

Napoli, Italy
Investigational Site Number : 380011
RECRUITING

Padua, Padova, 35128, Italy
Investigational Site Number : 380012
RECRUITING

Roma, Italy
Investigational Site Number : 380013
RECRUITING

Messina, 98125, Italy
Investigational Site Number : 380014
RECRUITING

Ferrara, 44124, Italy
Investigational Site Number : 380015
RECRUITING

Roma, 00165, Italy
Investigational Site Number : 380016
RECRUITING

Milan, 20122, Italy
Investigational Site Number : 380017
RECRUITING

Torino, 10126, Italy
Investigational Site Number : 380019
RECRUITING

Napoli, Italy
Investigational Site Number : 392105
COMPLETED

Ginowan, Okinawa, 901-2214, Japan
Investigational Site Number : 392106
COMPLETED

Sakyo-ku, Kyoto, 606-8507, Japan
Investigational Site Number : 4000001
RECRUITING

Amman, 261, Jordan
Investigational Site Number : 4220004
RECRUITING

Beirut, 11072210, Lebanon
Investigational Site Number : 458001
RECRUITING

Kuala Pahang, 50586, Malaysia
Investigational Site Number : 458002
RECRUITING

Kuala Lumpur, 59100, Malaysia
Investigational Site Number : 608001
RECRUITING

Manila, 1000, Philippines
Investigational Site Number : 620006
RECRUITING

Lisbon, 1649-035, Portugal
Investigational Site Number : 620008
RECRUITING

Coimbra, 3000-075, Portugal
Investigational Site Number : 643002
COMPLETED

Moscow, 117218, Russia
Investigational Site Number : 682001
COMPLETED

Al Qaţīf, Saudi Arabia
Investigational Site Number : 682004
RECRUITING

Mecca, 21955, Saudi Arabia
Investigational Site Number : 6880001
COMPLETED

Belgrade, 11000, Serbia
Investigational Site Number : 702001
RECRUITING

Singapore, 229899, Singapore
Investigational Site Number : 703001
COMPLETED

Bratislava, 83340, Slovakia
Investigational Site Number : 704002
RECRUITING

Ho Chi Minh City, 700000, Vietnam
Investigational Site Number : 764001
RECRUITING

Bangkok, Thailand
Investigational Site Number : 764002
COMPLETED

Bangkok, 10400, Thailand
Investigational Site Number : 764003
RECRUITING

Bangkok, 10400, Thailand
Investigational Site Number : 764004
RECRUITING

Bangkok, 10700, Thailand
Investigational Site Number : 764005
RECRUITING

Khon Kaen, 40002, Thailand
Investigational Site Number : 7840001
RECRUITING

Dubai, United Arab Emirates
John Hopkins- Site Number : 840044
COMPLETED

Baltimore, Maryland, 21205, United States
LSD Data Registry Site LLC- Site Number : 840094
RECRUITING

Dublin, Ohio, 43017, United States
Loma Linda University- Genetics- Site Number : 840070
COMPLETED

Loma Linda, California, 92354, United States
Maine Medical Center Pediatrics- Site Number : 840064
RECRUITING

Portland, Maine, 04102, United States
Massachusetts General Hospital-Genetics- Site Number : 840062
RECRUITING

Boston, Massachusetts, 02114, United States
Metropolitan Hospital Center- Site Number : 840110
RECRUITING

New York, New York, 10029-7494, United States
Mt. Sinai School of Medicine- Site Number : 840005
RECRUITING

New York, New York, 10029, United States
Multicare Health System ¿ Mary Bridge Childrens Hospital- Site Number : 840115
RECRUITING

Tacoma, Washington, 98415, United States
Nationwide Children's Hospital - PIN- Site Number : 840091
RECRUITING

Columbus, Ohio, 43205-2664, United States
New York Medical College- Site Number : 840039
RECRUITING

Valhalla, New York, 10595, United States
New York University School Of Medicine- Site Number : 840040
RECRUITING

New York, New York, 10016, United States
Northwell Health- Site Number : 840102
RECRUITING

Manhasset, New York, 11030, United States
O&O Alpan, LLC- Site Number : 840025
RECRUITING

Fairfax, Virginia, 22030, United States
Oregon Health & Science University (OHSU)- Site Number : 840095
TERMINATED

Portland, Oregon, 97239, United States
Oregon Health & Sciences University- Site Number : 840080
RECRUITING

Portland, Oregon, 97201, United States
Oregon Health and Scinece University- Site Number : 840038
TERMINATED

Portland, Oregon, 97239, United States
Penn Hershey Medical Center- Site Number : 840061
COMPLETED

Hershey, Pennsylvania, 17033, United States
Penn State Health Milton South Hershey Medical Center- Site Number : 840126
RECRUITING

Hershey, Pennsylvania, 17033, United States
Phoenix Children's Hospital- Site Number : 840003
RECRUITING

Phoenix, Arizona, 85013, United States
Rhode Island Hospital Genetics- Site Number : 840053
COMPLETED

Providence, Rhode Island, 02903, United States
Rush University Medical Center Genetics- Site Number : 840079
RECRUITING

Chicago, Illinois, 60612, United States
Seattle Children's Hospital- Site Number : 840028
RECRUITING

Seattle, Washington, 98105, United States
Southern California Permanente Medical Group- Site Number : 840108
RECRUITING

Los Angeles, California, 90027, United States
Spectrum for Health- Site Number : 840019
COMPLETED

Grand Rapids, Michigan, 49503, United States
St. Joseph's Children's Hospital- Site Number : 840057
RECRUITING

Paterson, New Jersey, 07503, United States
St. Peter's University Hospital- Site Number : 840016
RECRUITING

New Brunswick, New Jersey, 08901, United States
Stanford University Pediatrics- Site Number : 840021
RECRUITING

Stanford, California, 94305, United States
State University of New York- Site Number : 840052
RECRUITING

Syracuse, New York, 13210, United States
UC Davis MIND Institute- Site Number : 840010
RECRUITING

Sacramento, California, 95817, United States
UPMC- Site Number : 840014
RECRUITING

Pittsburgh, Pennsylvania, 15213, United States
USC Health Sciences Center Dept of Genetics- Site Number : 840082
COMPLETED

Los Angeles, California, 90033, United States
University Alabama at Birmingham- Site Number : 840106
RECRUITING

Birmingham, Alabama, 35233, United States
University Hospitals Cleveland Medical Center- Site Number : 840119
RECRUITING

Cleveland, Ohio, 44106, United States
University Of Miami SOM- Site Number : 840006
RECRUITING

Miami, Florida, 33136, United States
University Of Washington Medical Center- Site Number : 840059
RECRUITING

Seattle, Washington, 98195, United States
University of Arizona- Site Number : 840015
RECRUITING

Tucson, Arizona, 85724, United States
University of Arkansas for Medical Sciences- Site Number : 840113
RECRUITING

Little Rock, Arkansas, 72205, United States
University of California at Irvine- Site Number : 840036
RECRUITING

Irvine, California, 90211, United States
University of California at San Diego- Site Number : 840007
COMPLETED

San Diego, California, 92093, United States
University of California at San Francisco- Site Number : 840051
RECRUITING

San Francisco, California, 94143-0748, United States
University of Cincinnati Medical Center- Site Number : 840124
RECRUITING

Cincinnati, Ohio, 45219, United States
University of Colorado at Denver Genetics- Site Number : 840068
RECRUITING

Aurora, Illinois, 80045, United States
University of Florida College of Medicine- Site Number : 840012
RECRUITING

Gainesville, Florida, 32610, United States
University of Florida Pediatrics Genetics- Site Number : 840121
RECRUITING

Jacksonville, Florida, 32207, United States
University of Florida-Genetics- Site Number : 840096
RECRUITING

Tampa, Florida, 33606, United States
University of Iowa- Site Number : 840032
RECRUITING

Iowa City, Iowa, 52242, United States
University of Kansas Medical Center- Site Number : 840020
RECRUITING

Kansas City, Kansas, 66160, United States
University of Louisville- Genetics- Site Number : 840030
COMPLETED

Louisville, Kentucky, 40202, United States
University of Michigan Pediatrics- Site Number : 840107
RECRUITING

Ann Arbor, Michigan, 48109, United States
University of Minnesota Medical Center Pediatrics- Site Number : 840035
RECRUITING

Minneapolis, Minnesota, 55455, United States
University of Minnesota Medical Center Pediatrics- Site Number : 840076
RECRUITING

Minneapolis, Minnesota, 55455, United States
University of Missouri Health System Department of Genetics- Site Number : 840031
RECRUITING

Columbia, Missouri, 65212, United States
University of Nebraska Medical Center- Pediatrics- Site Number : 840084
RECRUITING

Omaha, Nebraska, 68198, United States
University of Pittsburgh- Site Number : 840023
RECRUITING

Pittsburgh, Pennsylvania, 15224, United States
University of Rochester Medical Center SOM- Site Number : 840105
COMPLETED

Rochester, New York, 14642, United States
University of Utah Department of Medical Genetics- Site Number : 840043
RECRUITING

Salt Lake City, Utah, 84132, United States
University of Virginia School of Medicine-Pediatrics- Site Number : 840078
COMPLETED

Charlottesville, Virginia, 22908, United States
Vanderbilt University Hospital-Pediatrics- Site Number : 840049
RECRUITING

Nashville, Tennessee, 38232, United States
Washington University of St. Louis- Site Number : 840100
RECRUITING

St Louis, Missouri, 63110, United States
Yale - Site Number : 840047
RECRUITING

New Haven, Connecticut, 06520, United States

Conditions

Explore the condition pages connected to this study.

GLYCOGEN STORAGE DISEASE TYPE II POMPE DISEASE