Oral pill challenge to injection for rare blood disease shows promise

NCT ID NCT06799546

Summary

This completed Phase 3 trial tested if a new oral tablet called HSK39297 could work as well as the standard injected drug (eculizumab) for people with a rare blood disease called PNH who had never tried this type of medicine before. The main goal was to see if the pill could safely raise and maintain patients' hemoglobin levels without needing blood transfusions. Researchers directly compared the two treatments in 73 adult patients to measure which was better at controlling the disease.

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Contacts and locations

Locations

  • The First Affiliated Hospital of Nanjing Medical University

    Nanjing, Jiangsu, 210029, China

  • The First Affiliated Hospital, College of Medicine, Zhejiang University

    Hangzhou, Zhejiang, 310003, China

Conditions

Explore the condition pages connected to this study.