New hope for kids with rare blood disorder

NCT ID NCT06449001

Summary

This study is testing whether adding a new drug called danicopan helps children with a rare blood disease called PNH. The children are already on standard treatment but still have significant anemia. The main goal is to see if the add-on drug increases their hemoglobin levels (a measure of red blood cells) after 12 weeks.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Research Site

    RECRUITING

    Saskatoon, Saskatchewan, S7N 0W8, Canada

  • Research Site

    RECRUITING

    Paris, 77019, France

  • Research Site

    RECRUITING

    Leeds, LS9 7TF, United Kingdom

  • Research Site

    RECRUITING

    London, SE5 9RS, United Kingdom

Conditions

Explore the condition pages connected to this study.