New hope for kids with rare blood disorder
NCT ID NCT06449001
Summary
This study is testing whether adding a new drug called danicopan helps children with a rare blood disease called PNH. The children are already on standard treatment but still have significant anemia. The main goal is to see if the add-on drug increases their hemoglobin levels (a measure of red blood cells) after 12 weeks.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Research Site
RECRUITINGSaskatoon, Saskatchewan, S7N 0W8, Canada
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Research Site
RECRUITINGParis, 77019, France
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Research Site
RECRUITINGLeeds, LS9 7TF, United Kingdom
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Research Site
RECRUITINGLondon, SE5 9RS, United Kingdom
Conditions
Explore the condition pages connected to this study.