New drug offers hope for rare, severe high triglyceride conditions

NCT ID NCT06796426

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This program gives adults and adolescents with familial chylomicronemia syndrome (FCS) and adults with severe hypertriglyceridemia (SHTG) access to an experimental drug called plozasiran. Participants receive injections every 3 months for 15 to 21 months. The goal is to lower dangerously high triglyceride levels that standard treatments haven't controlled.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance
plozasiran (a drug injection)
What this could lead to
If it works, this could provide a treatment option for people with severe high triglycerides who haven't responded to standard therapy.
What could go wrong
This is an expanded access program, not a controlled trial, so results are less certain. The drug may not work for everyone and could have side effects.

This is an AI summary of the original study and may miss details. Read our disclaimer.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for FAMILIAL CHYLOMICRONEMIA are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Arrowhead Pharmaceuticals, Inc.

    AVAILABLE

    Pasadena, California, 91105, United States

More trials for these conditions

Other studies related to the condition(s) this trial covers.