Scientists watch and learn from rare kidney disease

NCT ID NCT04982393

Summary

This study aims to better understand the natural course of Primary Hyperoxaluria Type 1 (PH1), a rare genetic disorder that causes kidney stones and kidney damage. Researchers will observe 207 patients already diagnosed with PH1 to see how the disease progresses over time in the real world. A key part of the study is to monitor the long-term safety and effectiveness of the drug lumasiran in patients who are taking it as part of their regular care.

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Contacts and locations

Locations

  • Clinical Trial Site

    Phoenix, Arizona, 85016, United States

  • Clinical Trial Site

    Washington D.C., District of Columbia, 20010, United States

  • Clinical Trial Site

    Boston, Massachusetts, 02115, United States

  • Clinical Trial Site

    Rochester, Minnesota, 55905, United States

  • Clinical Trial Site

    Cincinnati, Ohio, 45229, United States

  • Clinical Trial Site

    Pittsburgh, Pennsylvania, 15213, United States

  • Clinical Trial Site

    Dallas, Texas, 75390, United States

  • Clinical Trial Site

    Houston, Texas, 77030, United States

  • Clinical Trial Site

    Ghent, Belgium

  • Clinical Trial Site

    Liège, Belgium

  • Clinical Trial Site

    Hamilton, Ontario, Canada

  • Clinical Trial Site

    Toronto, Ontario, Canada

  • Clinical Trial Site

    Laurier, Quebec, Canada

  • Clinical Trial Site

    Bordeaux, France

  • Clinical Trial Site

    Lyon, France

  • Clinical Trial Site

    Paris, France

  • Clinical Trial Site

    Berlin, Germany

  • Clinical Trial Site

    Cologne, Germany

  • Clinical Trial Site

    Hamburg, Germany

  • Clinical Trial Site

    Jerusalem, Israel

  • Clinical Trial Site

    Orbassano, Torino, Italy

  • Clinical Trial Site

    Milan, Italy

  • Clinical Trial Site

    Verona, Italy

  • Clinical Trial Site

    Amsterdam, Netherlands

  • Clinical Trial Site

    Santa Cruz de Tenerife, Canary Islands, Spain

  • Clinical Trial Site

    Barcelona, Spain

  • Clinical Trial Site

    Las Palmas, Spain

  • Clinical Trial Site

    Bern, Switzerland

  • Clinical Trial Site

    London, England, United Kingdom

  • Clinical Trial Site

    London, United Kingdom

Conditions

Explore the condition pages connected to this study.