Lab test could predict which cystic fibrosis patients benefit from drug

NCT ID NCT03894657

Summary

This study aimed to see if a laboratory test on patients' own nasal cells could predict how well they would respond to the cystic fibrosis drug Orkambi. Researchers tested 91 patients with a specific genetic form of cystic fibrosis who were starting Orkambi treatment. They compared results from the nasal cell test to actual improvements in patients' lung function over 24-48 weeks of treatment.

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Contacts and locations

Locations

  • Hôpital Necker-Enfants Malades

    Paris, Île-de-France Region, 75015, France

Conditions

Explore the condition pages connected to this study.