Breakthrough injection shows promise for devastating kidney conditions

NCT ID NCT05067127

Summary

This Phase 3 study tested whether pegcetacoplan injections could help people with rare kidney diseases called C3 glomerulopathy (C3G) or immune-complex membranoproliferative glomerulonephritis (IC-MPGN). The trial involved 124 participants who received either the actual drug or placebo injections twice weekly for 26 weeks. Researchers measured whether the treatment reduced protein in urine and helped preserve kidney function.

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Contacts and locations

Locations

  • ASST Grande Ospedale Metropolitano Niguarda

    Milan, 20162, Italy

  • Academic Medical Research Institute

    Los Angeles, California, 90022, United States

  • Aichi Children's Health and Medical Center

    Ōbu, Aichi-ken, 474-8710, Japan

  • Azienda Ospedaliera Universitaria di Padova (39011)

    Padua, 35128, Italy

  • Boston Children's Hospital (01013)

    Boston, Massachusetts, 02115, United States

  • CHU Montpellier, Hopital Lapeyronie

    Montpellier, 34295, France

  • CHU Sart-Tilman

    Liège, B-4000, Belgium

  • CHU de Bordeaux - Hopital Pellegrin

    Bordeaux, 33076, France

  • CHU de Saint Etienne, Hospital Nord

    Saint-Priest-en-Jarez, 42055, France

  • CHUV Lausanne

    Lausanne, CH-1011, Switzerland

  • CUIMC - Columbia Nephrology

    New York, New York, 10032, United States

  • Canberra Hospital - Renal Clinical Trials & Research Unit

    Garran, Australian Capital Territory, 2605, Australia

  • Catholic University of Leuven

    Leuven, B-3000, Belgium

  • Centro de Tratamento de Doencas Renais

    Juiz de Fora, Minas Gerais, 36025-340, Brazil

  • Charite Universitatsmedizin (49007)

    Berlin, 10117, Germany

  • Children's Hospital Colorado

    Aurora, Colorado, 80045, United States

  • Children's Mercy Hospital

    Kansas City, Missouri, 64102, United States

  • Clinica Privada Velez Sarsfield

    Córdoba, X5000, Argentina

  • Clinical Trials CHU de Liège

    Liège, B-4000, Belgium

  • Cohen Children Hospital

    New Hyde Park, New York, 11040, United States

  • Emma Kinderziekenhuis, Amsterdam UMC

    Amsterdam, 1105 AZ, Netherlands

  • Emory University School of Medicine

    Atlanta, Georgia, 30322, United States

  • Evelina London Children Hospital (44016)

    London, SE1 7EH, United Kingdom

  • Faculty Hospital Kralovske Vinohrady (42002)

    Prague, Czechia

  • Fides Clinical Research, LLC (01042)

    Atlanta, Georgia, 30342, United States

  • Fundació Puigvert

    Barcelona, 08025, Spain

  • Gloucestershire Hospitals NHS Foundation Trust

    Gloucester, GL1 3NN, United Kingdom

  • Great Ormond Street Hospital Foundation Trust

    London, WC1N 3JH, United Kingdom

  • Gunma University Hospital (81006)

    Maebashi, Gunma, 371-8511, Japan

  • HC UNESP Botucatu

    Botucatu, 18618-687, Brazil

  • HCFMUSP-Hospital Clinicas da Faculdade Medicina da Universidade de São Paulo

    São Paulo, 05403-900, Brazil

  • Hackensack Meridian Health

    Hackensack, New Jersey, 07601, United States

  • Hopital Erasme HUB Service Pharmacie

    Brussels, 1070, Belgium

  • Hopital Henri-Mondor

    Créteil, 94010, France

  • Hopital Maisonneuve-Rosemont

    Montreal, Quebec, QC H1T2M4, Canada

  • Hopital Necker (33014)

    Paris, 75015, France

  • Hospital Edouard Herriot, Hospices Civils de Lyon

    Lyon, 69437, France

  • Hospital Materno Infantil Sant Joan de Deu

    Barcelona, 08950, Spain

  • Hospital Privado-Universitario de Cordoba

    Córdoba, CPA X5016KEH, Argentina

  • Hospital Universitari Vall D'Hebron

    Barcelona, 08035, Spain

  • Hospital Universitario 12 de Octubre, Nephrology Department

    Madrid, 28041, Spain

  • Hospital Universitario Austral

    Buenos Aires, 1629, Argentina

  • Hospital Universitario Dr Peset

    Valencia, 46017, Spain

  • Hospital Universitario Marques de Valdecilla

    Santander, 39008, Spain

  • Hospital Universitario Materno-Infantil Vall d' Hebron, Nefrologia Pediatrica

    Barcelona, 08035, Spain

  • Hospital Universitario Walter Cantidio

    Fortaleza, 60430-372, Brazil

  • Hospital das Clinicas de Ribeirao Preto, Division of Nephrology

    Ribeirão Preto, 14110-000, Brazil

  • Hospital de Base

    São José do Rio Preto, 150900-000, Brazil

  • Hospital de Clinicas de Porto Alegre

    Porto Alegre, 90035-903, Brazil

  • Hospital for Sick Children (11003)

    Toronto, Ontario, M5G 1X8, Canada

  • Hôpital Européen Georges-Pompidou

    Paris, 75015, France

  • IRCCS Istituto Giannina Gaslini (39012)

    Genova, 16147, Italy

  • Imperial College Healthcare NHS Trust

    London, W12 0HS, United Kingdom

  • Inselspital, Bern University Hospital

    Bern, CH-3010, Switzerland

  • Institute for Clinical and Experimental Medicine

    Prague, 140 21, Czechia

  • Institute for Public Health and Medicine Northwestern University Northwestern University (01041)

    Chicago, Illinois, 60611, United States

  • Institute of Pediatric Nephrology

    Petah Tikva, 4920235, Israel

  • Instituti Clinici Scientifici Maugeri SPA-IRCCS

    Pavia, 27100, Italy

  • Instituto da Crianca-Hospital das Clinicas University of Sao Paulo

    São Paulo, 05403-000, Brazil

  • Irmandade da Santa Casa de Misericordia de Porto Alegre

    Porto Alegre, Rio Grande do Sul, 90020-090, Brazil

  • Irmandade da Santa Casa de Misericordia de Porto Alegre

    Porto Alegre, 90020-090, Brazil

  • Istituto di Ricerche Farmacologiche Mario Negri IRCCS

    Milan, 20156, Italy

  • Keck School of Medicine, University of Southern California

    Los Angeles, California, 90033, United States

  • Keimyung University Dongsan Medical Center

    Daegu, 42601, South Korea

  • Kitano Hospital

    Osaka, 530-8480, Japan

  • Kyorin University Hospital (81009)

    Tokyo, 181-8611, Japan

  • Lille Regional University Hospital Center, Claude Huriez Hospital, Department of Nephrology

    Paris, 59037, France

  • MedResearch Inc

    El Paso, Texas, 79902, United States

  • Medical University Hospital Innsbruck (43004)

    Innsbruck, 6020, Austria

  • Medizinische Hochschule Hannover, Studienzentrum fur Nieren und Hochdruckerkrankungen

    Hanover, 30625, Germany

  • Medizinische Universität Wien

    Vienna, A-1090, Austria

  • Monash University

    Box Hill, VIC 3128, Australia

  • NANIU Research Chicago (01040)

    Oak Brook, Illinois, 60523, United States

  • NHO Kanazawa Medical Center

    Kanazawa, Ishikawa-ken, 9208650, Japan

  • Nagasaki University Hospital (81005)

    Nagasaki, Nagasaki, 852-8501, Japan

  • Nagoya University Hospital (81003)

    Nagoya, Aichi-ken, 466-8560, Japan

  • Nantes University Hospital

    Nantes, 44093, France

  • Nefrologia I-Dor

    Rio de Janeiro, 22211-225, Brazil

  • Nephrology Associates of Northern IL and Inn (01043)

    Fort Wayne, Indiana, 46804, United States

  • Northeast Clinical Research Center, LLC

    Bethlehem, Pennsylvania, 18017, United States

  • Nottingham Children's Hospital

    Nottingham, NG7 2UH, United Kingdom

  • Oregon Health & Science University (01038)

    Portland, Oregon, 97239, United States

  • Ospedale Pediatrico Bambino Gesu

    Rome, 00165, Italy

  • Policlinico Sant Orsola-Malpighi

    Bologna, 40138, Italy

  • Policlinico di Bari

    Bari, 70123, Italy

  • Princess Alexandra Hospital

    Woolloongabba, Queensland, QLD 4102, Australia

  • Princess Alexandra Hospital

    Woolloongabba, QLD 4102, Australia

  • Radboud University Medical Center

    Nijmegen, 6500 HB, Netherlands

  • Rambam Health Care Campus

    Haifa, 3109601, Israel

  • Rangueil Hospital-University Hospital Center (CHU) of Toulouse

    Toulouse, 31059, France

  • Real Hospital Portuguas de Beneficancia em Pernambuco

    Recife, 52010-095, Brazil

  • Renal and Transplant Associates of New England, PC

    Springfield, Massachusetts, 01107, United States

  • Ronald Reagan UCLA Medical Center (01035)

    Los Angeles, California, 90095, United States

  • Royal Free London NHS Foundation Trust (44015)

    London, NW3 2QG, United Kingdom

  • Royal Manchester Children's Hospital

    Manchester, M13 9WL, United Kingdom

  • Ruschel Medicina E Pesquisa Clinica

    Rio de Janeiro, 22270-060, Brazil

  • SPZOZ Centralny Szpital Kliniczny Uniwersytetu Medycznego w Lodzi

    Lodz, 92-213, Poland

  • Samodzielny Publiczny Zaklad Opieki Zdrowotnej Uniwersytecki Szpital Kliniczny Nr 1 im. Norberta Barlickiego Uniwersytetu Medycznego w Lodzi

    Lodz, 90-153, Poland

  • Santa Casa de Misericordia de Belo Horizonte

    Belo Horizonte, Minas Gerais, 30150-221, Brazil

  • Seirei Hamamatsu General Hospital (81004)

    Hamamatsu, Shizuoka, 430-8558, Japan

  • Seoul National University Hospital

    Soeul, 03080, South Korea

  • Seoul National University Hospital (82005)

    Seoul, 3080, South Korea

  • St George'Äôs University Hospitals NHS Foundation Trust (44014)

    London, SW17 0QT, United Kingdom

  • St. Vincents Melbourne

    Fitzroy, VIC 3065, Australia

  • Texas Children's Hospital

    Houston, Texas, 77030, United States

  • The Ohio State University Medical Center

    Columbus, Ohio, 43210, United States

  • The University of Iowa

    Iowa City, Iowa, 52242, United States

  • UC Davis Medical Center (Transplant Research) (01016)

    Sacramento, California, 95817, United States

  • UCI Center for Clinical Research

    Orange, California, 92868, United States

  • UNIFESP - Hospital Sao Paulo

    São Paulo, 04038-002, Brazil

  • Universita degli Studi di Messina

    Messina, 98125, Italy

  • Universitatsklinikum Essen (AoR), Zentrum fur Kinder (49005)

    Essen, D-45147, Germany

  • Universitatsklinikum Munster

    Münster, 48149, Germany

  • Universitatsmedizin Mainz

    Mainz, 55131, Germany

  • Universitatsspital Zurich

    Zurich, CH-8091, Switzerland

  • University Hospital Antwerp (32004)

    Edegem, 2650, Belgium

  • University Hospital Regensburg (49004)

    Regensburg, 93053, Germany

  • University Hospital Strasbourg

    Strasbourg, 67091, France

  • University Hospital of Virgen del Rocio

    Seville, 41013, Spain

  • University Hospitals of Leicester NHS trust (44003)

    Leicester, LE1 5WW, United Kingdom

  • University Medical Center Groningen

    Groningen, 9713 GZ, Netherlands

  • University of Alabama at Birmingham

    Birmingham, Alabama, 35294, United States

  • University of Florida

    Gainesville, Florida, 32610, United States

  • University of Michigan Medical Center

    Ann Arbor, Michigan, 48109, United States

  • Yonsei University College of Medicine, Sinchon Severance Hospital

    Seoul, 03722, South Korea

Conditions

Explore the condition pages connected to this study.