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New hope for kids with rare Muscle-Weakening disease

NCT ID NCT06607627

Recruiting now Disease control Sponsor: Alexion Pharmaceuticals, Inc. Source: ClinicalTrials.gov ↗

Summary

This study is testing an investigational drug called gefurulimab in children and teenagers (ages 6 to under 18) who have generalized myasthenia gravis (gMG), a condition that causes severe muscle weakness. The main goals are to see how the drug behaves in the body, if it is safe, and if it helps improve muscle strength and daily activities. It is an open-label study, meaning all participants will receive the drug, and researchers will track their progress for at least 18 weeks.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Research Site

    RECRUITING

    Washington D.C., District of Columbia, 20010, United States

  • Research Site

    RECRUITING

    Norfolk, Virginia, 23507, United States

  • Research Site

    RECRUITING

    Joinville, 89202-451, Brazil

  • Research Site

    RECRUITING

    Salvador, 41253-190, Brazil

  • Research Site

    RECRUITING

    São José do Rio Preto, 15090-000, Brazil

  • Research Site

    RECRUITING

    São Paulo, 0438-002, Brazil

  • Research Site

    RECRUITING

    São Paulo, 05403-000, Brazil

  • Research Site

    RECRUITING

    Saitama-Shi, 330-8777, Japan

  • Research Site

    NOT_YET_RECRUITING

    Bydgoszcz, 85-065, Poland

  • Research Site

    WITHDRAWN

    Lodz, 93-338, Poland

  • Research Site

    RECRUITING

    Warsaw, 02-097, Poland

  • Research Site

    RECRUITING

    New Taipei City, 23561, Taiwan

  • Research Site

    RECRUITING

    Taipei, 11101, Taiwan

Conditions

Explore the condition pages connected to this study.

GENERALIZED MYASTHENIA GRAVIS GMG