New pill could stop debilitating HAE attacks in their tracks

NCT ID NCT02303626

First seen Nov 17, 2025 · Last updated May 24, 2026 · Updated 21 times

Summary

This study tested an oral medication called BCX4161 to prevent sudden swelling attacks in people with hereditary angioedema (HAE), a rare genetic condition. About 110 adults with HAE type I or II took either a low dose, high dose, or placebo daily for 12 weeks. Researchers tracked how many attacks occurred and how many days were attack-free to see if the drug works better than a placebo.

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Contacts and locations

Locations

  • Study site

    Birmingham, Alabama, 35209, United States

  • Study site

    Scottsdale, Arizona, 85251, United States

  • Study site

    Granada Hills, California, 91344, United States

  • Study site

    San Diego, California, 92093, United States

  • Study site

    San Diego, California, 92112, United States

  • Study site

    Walnut Creek, California, 94598, United States

  • Study site

    Colorado Springs, Colorado, 80907, United States

  • Study site

    Shreveport, Louisiana, 71106, United States

  • Study site

    Chevy Chase, Maryland, 20815, United States

  • Study site

    Boston, Massachusetts, 02114, United States

  • Study site

    Plymouth, Minnesota, 55446, United States

  • Study site

    St Louis, Missouri, 63141, United States

  • Study site

    New York, New York, 10029, United States

  • Study site

    Charlotte, North Carolina, 28277, United States

  • Study site

    Cincinnati, Ohio, 45267, United States

  • Study site

    Oklahoma City, Oklahoma, 73131, United States

  • Study site

    Tulsa, Oklahoma, 74133, United States

  • Study site

    Lake Oswego, Oregon, 97035, United States

  • Study site

    Hershey, Pennsylvania, 17033, United States

  • Study site

    Pittsburgh, Pennsylvania, 15241, United States

  • Study site

    Dallas, Texas, 75231, United States

  • Study site

    Galveston, Texas, 77555, United States

  • Study site

    Fairfax, Virginia, 63141, United States

  • Study site

    Spokane, Washington, 99204, United States

  • Study site

    Tacoma, Washington, 98405, United States

  • Study site

    Leuven, Belgium

  • Study site

    Ottawa, Canada

  • Study site

    Grenoble, France

  • Study site

    Lille, France

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    Paris, France

  • Study site

    Berlin, Germany

  • Study site

    Frankfurt, Germany

  • Study site

    Mörfelden-Walldorf, Germany

  • Study site

    Budapest, Hungary

  • Study site

    Milan, Italy

  • Study site

    Birmingham, United Kingdom

  • Study site

    Bristol, United Kingdom

  • Study site

    Cardiff, United Kingdom

  • Study site

    London, United Kingdom

  • Study site

    Manchester, United Kingdom

Conditions

Explore the condition pages connected to this study.