New pill aims to tame rare, debilitating blood disease

NCT ID NCT06764303

Summary

This study is testing an experimental capsule called NTQ5082 for adults with paroxysmal nocturnal hemoglobinuria (PNH), a rare and serious blood disease. The main goal is to see if the pill can safely and effectively raise patients' hemoglobin levels, reduce the need for blood transfusions, and control other disease symptoms. It is a Phase 2 trial involving about 24 participants who have not taken similar complement inhibitor drugs before.

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Contacts and locations

Locations

  • Hematology Hospital of the Chinese Academy of Medical Sciences

    Tianjin, Tianjin Municipality, 250033, China

  • The First Affiliated Hospital, College of Medicine, Zhejiang University

    Hangzhou, Zhejiang, 310012, China

Conditions

Explore the condition pages connected to this study.