New pill trial offers hope for controlling debilitating blood disease

NCT ID NCT07177859

Summary

This study is testing an experimental oral medication called NTQ5082 for people with paroxysmal nocturnal hemoglobinuria (PNH), a rare and serious blood disease. It will compare NTQ5082 against an existing standard treatment to see if it's better at raising and maintaining hemoglobin levels, reducing the need for blood transfusions. The main goal is to see if patients can reach healthier hemoglobin levels for a sustained period without receiving any red blood cell transfusions.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences

    Tianjin, Tianjin Municipality, 300020, China

    Contact

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Conditions

Explore the condition pages connected to this study.