One-Shot gene therapy aims to tame debilitating swelling disorder

NCT ID NCT05120830

Summary

This early-stage study is testing a single injection of an experimental gene therapy called NTLA-2002 in adults with hereditary angioedema (HAE). The main goals are to see if the treatment is safe and if it can reduce the number of painful, unpredictable swelling attacks people experience. Researchers will monitor participants closely for side effects and track how many HAE attacks occur over several months.

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Contacts and locations

Locations

  • Clinical Trial Site

    Campbelltown, Australia

  • Clinical Trial Site

    Grenoble, France

  • Clinical Trial Site

    Lille, France

  • Clinical Trial Site

    Paris, France

  • Clinical Trial Site

    Berlin, Germany

  • Clinical Trial Site

    Frankfurt, Germany

  • Clinical Trial Site

    Amsterdam, Netherlands

  • Clinical Trial Site

    Auckland, New Zealand

  • Clinical Trial Site

    Cambridge, United Kingdom

Conditions

Explore the condition pages connected to this study.