New hope for rare genetic disorder: major trial tests daily pill for kids

NCT ID NCT07281079

Summary

This study is testing whether a daily oral medicine called NNZ-2591 can help children with Phelan-McDermid syndrome. It will compare the drug to a placebo in about 160 children aged 3 to 12. The main goals are to see if the medicine improves overall symptoms and communication skills over time.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Neuren PMS-301 Site#101

    RECRUITING

    New York, New York, 10029, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Neuren PMS-301 Site#109

    RECRUITING

    Chevy Chase, Maryland, 20815, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Neuren PMS-301 Site#111

    RECRUITING

    San Rafael, California, 94903, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.