New drug trial aims to help SMA patients walk farther

NCT ID NCT05794139

Summary

This study is testing whether an experimental drug called NMD670 can help adults with spinal muscular atrophy type 3 walk farther and improve muscle strength. Researchers will compare NMD670 against a placebo in 54 participants who can walk at least 50 meters without assistance. The main goal is to see if the drug increases how far people can walk in six minutes.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • AOU Città della Salute e della Scienza di Torino

    RECRUITING

    Torino, Italy

    Contact Email: •••••@•••••

  • Aarhus Universitetshospital, Neurologisk Afdeling

    RECRUITING

    Aarhus, Denmark

    Contact Email: •••••@•••••

  • CHR de la Citadelle - Neurologie

    RECRUITING

    Liège, Belgium

  • Charite - Campus Virchow-Klinikum (CVK)

    RECRUITING

    Berlin, Germany

  • Genge Partners Inc.

    RECRUITING

    Montreal, Canada

    Contact Email: •••••@•••••

  • H. Donostia

    WITHDRAWN

    Donostia / San Sebastian, Spain

  • Heritage Medical Research Clinic

    RECRUITING

    Calgary, Canada

    Contact Email: •••••@•••••

  • Hospital Materno Infantil La Paz

    RECRUITING

    Madrid, Spain

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Hospital Universitari Vall D Hebron

    RECRUITING

    Barcelona, Spain

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Hospital Universitario y Politécnico La Fe

    RECRUITING

    Valencia, Spain

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Istituto Giannina Gaslini, IRCCS

    RECRUITING

    Genova, Italy

  • Istituto Neurologico C. Besta, Fondazione IRCCS

    RECRUITING

    Milan, Italy

  • Neurology Rare Disease Center

    RECRUITING

    Denton, Texas, 76208, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Ospedale Niguarda, ASST Grande Ospedale Metropolitano Niguarda

    RECRUITING

    Milan, Italy

  • PU A. Gemelli, Università Cattolica del Sacro Cuore

    WITHDRAWN

    Roma, Italy

  • Rare Disease Center

    WITHDRAWN

    Atlanta, Georgia, 30329, United States

  • Rare Disease Research - Raleigh-Durham

    RECRUITING

    Hillsborough, North Carolina, 27278, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Rigshospitalet - Neurologisk Afdeling

    RECRUITING

    Copenhagen, Denmark

    Contact Email: •••••@•••••

  • Roy Blunt NextGen Precision Health Institute

    RECRUITING

    Columbia, Missouri, 65212, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Stanford University Medical Center

    RECRUITING

    Palo Alto, California, 94304, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The Johns Hopkins Medicine, Spinal Muscular Atrophy Center

    RECRUITING

    Baltimore, Maryland, 21287, United States

    Contact Email: •••••@•••••

  • The Ohio State University Wexner Medical Center

    RECRUITING

    Columbus, Ohio, 43210, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • UCLA David Geffen School Of Medicine - Neurology

    RECRUITING

    Los Angeles, California, 90095, United States

  • UF Fixel Institute for Neurological Diseases

    WITHDRAWN

    Gainesville, Florida, 32608, United States

  • UZ Leuven - Neurochirurgie Campus Gasthuisberg

    RECRUITING

    Leuven, Belgium

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Universitair Medisch Centrum Utrecht, locatie Academisch Zie - Neurology

    RECRUITING

    Utrecht, Netherlands

  • University of Colorado Neurology Clinic

    WITHDRAWN

    Aurora, Colorado, 80045, United States

  • University of Kansas Medical Center

    RECRUITING

    Kansas City, Kansas, 66160, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Università degli studi di Pisa

    WITHDRAWN

    Pisa, Italy

  • Universitätsklinikum Essen - Klinik Für Neurologie

    RECRUITING

    Essen, Germany

    Contact Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Washington University School of Medicine

    RECRUITING

    St Louis, Missouri, 63110, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.