New drug aims to boost walking ability in adults with muscle-weakening disease

NCT ID NCT05794139

First seen Nov 01, 2025 · Last updated May 14, 2026 · Updated 34 times

Summary

This study tests an experimental drug called NMD670 in 54 adults with type 3 spinal muscular atrophy, a condition that causes muscle weakness. Participants take the drug or a placebo for a period, then switch, to see if the drug improves walking distance and muscle strength. The goal is to find a safe treatment that eases symptoms and improves daily function.

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Contacts and locations

Locations

  • AOU Città della Salute e della Scienza di Torino

    Torino, Italy

  • Aarhus Universitetshospital, Neurologisk Afdeling

    Aarhus, Denmark

  • CHR de la Citadelle - Neurologie

    Liège, Belgium

  • Charite - Campus Virchow-Klinikum (CVK)

    Berlin, Germany

  • Genge Partners Inc.

    Montreal, Canada

  • Heritage Medical Research Clinic

    Calgary, Canada

  • Hospital Materno Infantil La Paz

    Madrid, Spain

  • Hospital Universitari Vall D Hebron

    Barcelona, Spain

  • Hospital Universitario y Politécnico La Fe

    Valencia, Spain

  • Istituto Giannina Gaslini, IRCCS

    Genova, Italy

  • Istituto Neurologico C. Besta, Fondazione IRCCS

    Milan, Italy

  • Neurology Rare Disease Center

    Denton, Texas, 76208, United States

  • Ospedale Niguarda, ASST Grande Ospedale Metropolitano Niguarda

    Milan, Italy

  • Rare Disease Research - Raleigh-Durham

    Hillsborough, North Carolina, 27278, United States

  • Rigshospitalet - Neurologisk Afdeling

    Copenhagen, Denmark

  • Roy Blunt NextGen Precision Health Institute

    Columbia, Missouri, 65212, United States

  • Stanford University Medical Center

    Palo Alto, California, 94304, United States

  • The Johns Hopkins Medicine, Spinal Muscular Atrophy Center

    Baltimore, Maryland, 21287, United States

  • The Ohio State University Wexner Medical Center

    Columbus, Ohio, 43210, United States

  • UCLA David Geffen School Of Medicine - Neurology

    Los Angeles, California, 90095, United States

  • UZ Leuven - Neurochirurgie Campus Gasthuisberg

    Leuven, Belgium

  • Universitair Medisch Centrum Utrecht, locatie Academisch Zie - Neurology

    Utrecht, Netherlands

  • University of Kansas Medical Center

    Kansas City, Kansas, 66160, United States

  • Universitätsklinikum Essen - Klinik Für Neurologie

    Essen, Germany

  • Washington University School of Medicine

    St Louis, Missouri, 63110, United States

Conditions

Explore the condition pages connected to this study.