Study on rare disease treatment withdrawn before starting
NCT ID NCT06227429
Summary
This study aimed to collect information on how children in China with a rare, serious liver disease (hereditary tyrosinemia type 1) fare while taking the medication nitisinone during their normal doctor visits. It was an observational study, meaning it would not test a new treatment but simply watch and record what happened. The study was withdrawn before any patients could be enrolled.
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Contacts and locations
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Locations
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Swedish Orphan Biovitrum Research Site
Beijing, China
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Swedish Orphan Biovitrum Research Site
Chongqing, China
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Swedish Orphan Biovitrum Research Site
Hefei, China
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Swedish Orphan Biovitrum Research Site
Wuhan, China
Conditions
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