HT-1 drug study in china: just watching, no new treatment

NCT ID NCT06227429

First seen Jan 06, 2026 · Last updated Apr 28, 2026 · Updated 18 times

Summary

This study was designed to observe patients with hereditary tyrosinemia type 1 (HT-1) in China who are already taking nitisinone. The goal was to track side effects, deaths, liver transplants, and liver cancer. However, the study was withdrawn before enrolling anyone, so no results were collected.

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Contacts and locations

Locations

  • Swedish Orphan Biovitrum Research Site

    Beijing, China

  • Swedish Orphan Biovitrum Research Site

    Chongqing, China

  • Swedish Orphan Biovitrum Research Site

    Hefei, China

  • Swedish Orphan Biovitrum Research Site

    Wuhan, China

Conditions

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